Nonrandomized Allocation of Steroid Therapy in Patients With Fukuyama Congenital Muscular Dystrophy: Study Protocol for a Phase <scp>II</scp> Clinical Trial
Based on previous clinical research, prednisolone shows great potential as a therapeutic drug in patients with FCMD. To achieve this goal, we planned an investigator-initiated trial to confirm the effectiveness and safety of prednisolone.
Authors
- Kenji Hatano (ORCID: https://orcid.org/0000-0001-7079-8247)
- Hideki Oi (ORCID: https://orcid.org/0009-0000-6005-0016)
- Takatoshi Sato
- Ryosuke Bo (ORCID: https://orcid.org/0000-0002-8931-7842)
- Minobu Shichiji
- Takami Ishizuka (ORCID: https://orcid.org/0000-0003-3641-3328)
- Mariko Taniguchi‐Ikeda (ORCID: https://orcid.org/0000-0002-1607-400X)
- Hiroyuki Awano (ORCID: https://orcid.org/0000-0001-9846-4142)
- Keiko Ishigaki (ORCID: https://orcid.org/0000-0001-8435-7418)
- Hisateru Tachimori (ORCID: https://orcid.org/0000-0001-6401-2885)
- Harumasa Nakamura (ORCID: https://orcid.org/0000-0002-1363-5000)
- Yuki Kihara (ORCID: https://orcid.org/0009-0003-9355-5397)
- Mari S. Oba (ORCID: https://orcid.org/0000-0001-8374-8038)
- Yasuhiro Takeshima (ORCID: https://orcid.org/0000-0002-6468-7185)
- Satoru Nagata
- Yuko Shimizu‐Motohashi
- Ayako Hattori (ORCID: https://orcid.org/0000-0003-2639-424X)
- Hiroko Harada
- Terumi Murakami
- K. Ishiguro
Institutions
- Hyogo Medical University (JP)
- Keio University (JP)
- Nagoya City University (JP)
- National Center of Neurology and Psychiatry (JP)
- Keio University Hospital (JP)
- Tottori University Hospital (JP)
- Fujita Health University Hospital (JP)
- Tokyo Women's Medical University (JP)
- National Hospital Organization (JP)
- Nagoya Medical Center (JP)
- Nagoya University (JP)
- Kobe University (JP)
- Hyogo University (JP)
Publication Details
- Journal
- Neuropsychopharmacology Reports
- Published
- 2025-08-15
- DOI
- https://doi.org/10.1002/npr2.70043
- Citations
- 1
- Primary Topic
- Muscle Physiology and Disorders
- Type
- article
- Field-Weighted Citation Impact
- 0.81
Funders
- Japan Agency for Medical Research and Development