Authors

• Don P. Wilson (ORCID: https://orcid.org/0000-0002-2815-4816)
• Manisha Balwani (ORCID: https://orcid.org/0000-0001-8047-5011)
• Lorenzo D’Antiga (ORCID: https://orcid.org/0000-0001-7150-3148)
• William F. Balistreri (ORCID: https://orcid.org/0000-0002-7051-8839)
• Emilio Ros (ORCID: https://orcid.org/0000-0002-2573-1294)
• Jennifer Evans (ORCID: https://orcid.org/0000-0002-6137-2030)
• Florian Abel

Institutions

• Cincinnati Children's Hospital Medical Center (US)
• Cook Children's Medical Center (US)
• Ospedale Papa Giovanni XXIII (IT)
• AstraZeneca (Brazil) (BR)
• Alexion Pharmaceuticals (United States) (US)
• AstraZeneca (United States) (US)
• Consorci Institut D'Investigacions Biomediques August Pi I Sunyer (ES)
• Alexion Pharma (Switzerland) (CH)
• University of Milano-Bicocca (IT)
• Icahn School of Medicine at Mount Sinai (US)

Publication Details

Journal

Liver International

Published

2025-08-08

DOI

https://doi.org/10.1111/liv.70279

Citations

2

Primary Topic

Lysosomal Storage Disorders Research

Type

article

Field-Weighted Citation Impact

2.33

Funders

• Alexion Pharmaceuticals