Myosin-ATPase inhibitor in real-world patients with obstructive HCM: a report by the Cardiomyopathies and Pericardial Diseases WG of the Italian Society of Cardiology

This study confirmed our recent demonstration that approximately half of real-world HOCM patients are suitable for Mavacamten therapy based on the full Explorer-HCM trial entry criteria. Due to the current limitation of compassionate use programmes in Italy, only one in four patients was admitted for treatment.

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Publication Details

Journal
Journal of Cardiovascular Medicine
Published
2025-06-20
DOI
https://doi.org/10.2459/jcm.0000000000001746
Citations
1
Primary Topic
Cardiomyopathy and Myosin Studies
Type
article
Field-Weighted Citation Impact
1.39
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article

Myosin-ATPase inhibitor in real-world patients with obstructive HCM: a report by the Cardiomyopathies and Pericardial Diseases WG of the Italian Society of Cardiology

Lorenzo‐Lupo Dei, Barbara Mabritto, Marco Merlo, Antonio J. Reginato et al.
1 citations
Journal of Cardiovascular Medicine
Cardiomyopathy and Myosin Studies
1.39
article

Myosin-ATPase inhibitor in real-world patients with obstructive HCM: a report by the Cardiomyopathies and Pericardial Diseases WG of the Italian Society of Cardiology

Lorenzo‐Lupo Dei, Barbara Mabritto, Marco Merlo, Antonio J. Reginato, Diego La Maestra, Silvia Castelletti, Denise Cristiana Faro, Beatrice Musumeci, Camillo Autore, Enrica Perugini, Fabio Vagnarelli, Emanuele Monda, Maria Alessandra Schiavo, Giancarlo Todiere, Francesco Negri, Iacopo Olivotto, Cesare de Gregorio, Giuseppe Patti, Federico Angriman, Ines Monte, Cinzia Forleo, Denisa Muraru, Mariapaola Campisi, Carla Lofiego, Massimo Mapelli, Giuseppe Limongelli, Valeria Rella, Massimo Imazio, Claudia Raineri, Aniello Sammartino, Marco Metra, Andrea Barison, Daniela Tomasoni, Giacomo Dattolo, Lia Crotti, Maurizio Sguazzotti, Chiara Calore, Giacomo Tini, Marco Canepa, Francesca Fumero, Elena Biagini, Vladyslav Chubuchnyi, Francesco Cappelli, Andrea Igoren Guaricci, Daniele Melis, P Tofoni, Maria Giulia Bellicini, Federica Verrillo, Paolo Bellocchi, Federica Re, Giuseppe Musumeci, Marika Martini, Gianfranco Sinagra, Alberto Aimo, Anna Maria Napoli, Claudio Bergami
article en
1 citations

Abstract

This study confirmed our recent demonstration that approximately half of real-world HOCM patients are suitable for Mavacamten therapy based on the full Explorer-HCM trial entry criteria. Due to the current limitation of compassionate use programmes in Italy, only one in four patients was admitted for treatment.

Journal of Cardiovascular MedicineVol. 26(7)
Università degli Studi del Piemonte Orientale “Amedeo Avogadro” (IT), University of Udine (IT), University of Padua (IT), University of Trieste (IT), Università degli studi di Cassino e del Lazio Meridionale (IT), University of Milan (IT), University of Campania "Luigi Vanvitelli" (IT), Fondazione IRCCS Ca' Granda Ospedale Maggiore Policlinico (IT), University of Catania (IT), Ospedale Maggiore (IT), Centro Cardiologico Monzino (IT), Fondazione Ricerca Molinette (IT), Surgical Specialties (Canada) (CA), Azienda Ospedaliero-Universitaria Careggi (IT), Azienda USL di Bologna (IT), Ospedale Santa Maria della Misericordia di Udine (IT), A. O. Ordine Mauriziano di Torino (IT), IRCCS Istituto Auxologico Italiano (IT), Nini Hospital (LB), ERN GUARD-Heart (NL), Istituti di Ricovero e Cura a Carattere Scientifico (IT), Piedmont University (US), Fondazione Toscana Gabriele Monasterio (IT), Azienda Sanitaria Universitaria Integrata di Trieste (IT), University of Bari Aldo Moro (IT), University of Milano-Bicocca (IT), University of Brescia (IT), University of Genoa (IT), Sapienza University of Rome (IT)
Good health and well-being
Openalex Percentile: Top 18%
Cardiomyopathy and Myosin Studies
1.39
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