Myosin-ATPase inhibitor in real-world patients with obstructive HCM: a report by the Cardiomyopathies and Pericardial Diseases WG of the Italian Society of Cardiology
This study confirmed our recent demonstration that approximately half of real-world HOCM patients are suitable for Mavacamten therapy based on the full Explorer-HCM trial entry criteria. Due to the current limitation of compassionate use programmes in Italy, only one in four patients was admitted for treatment.
Authors
- Lorenzo‐Lupo Dei (ORCID: https://orcid.org/0000-0002-1091-9390)
- Barbara Mabritto (ORCID: https://orcid.org/0000-0001-6678-1274)
- Marco Merlo
- Antonio J. Reginato
- Diego La Maestra
- Silvia Castelletti
- Denise Cristiana Faro (ORCID: https://orcid.org/0000-0002-6568-6176)
- Beatrice Musumeci (ORCID: https://orcid.org/0000-0003-4872-7981)
- Camillo Autore (ORCID: https://orcid.org/0000-0002-6542-7342)
- Enrica Perugini
- Fabio Vagnarelli (ORCID: https://orcid.org/0009-0006-0993-061X)
- Emanuele Monda (ORCID: https://orcid.org/0000-0001-9304-988X)
- Maria Alessandra Schiavo
- Giancarlo Todiere (ORCID: https://orcid.org/0000-0002-3459-026X)
- Francesco Negri (ORCID: https://orcid.org/0000-0003-2909-3928)
- Iacopo Olivotto (ORCID: https://orcid.org/0000-0003-1751-9266)
- Cesare de Gregorio (ORCID: https://orcid.org/0000-0003-3022-266X)
- Giuseppe Patti (ORCID: https://orcid.org/0000-0002-5404-3968)
- Federico Angriman (ORCID: https://orcid.org/0000-0003-0971-386X)
- Ines Monte (ORCID: https://orcid.org/0000-0001-7059-7525)
- Cinzia Forleo (ORCID: https://orcid.org/0000-0002-9452-4037)
- Denisa Muraru (ORCID: https://orcid.org/0000-0003-2514-3668)
- Mariapaola Campisi
- Carla Lofiego
- Massimo Mapelli (ORCID: https://orcid.org/0000-0001-9985-7407)
- Giuseppe Limongelli (ORCID: https://orcid.org/0000-0002-8291-9517)
- Valeria Rella (ORCID: https://orcid.org/0000-0001-8485-3649)
- Massimo Imazio (ORCID: https://orcid.org/0000-0002-5722-0245)
- Claudia Raineri (ORCID: https://orcid.org/0000-0001-9653-1516)
- Aniello Sammartino
- Marco Metra (ORCID: https://orcid.org/0000-0001-6691-8568)
- Andrea Barison (ORCID: https://orcid.org/0000-0001-9042-340X)
- Daniela Tomasoni (ORCID: https://orcid.org/0000-0002-7584-2857)
- Giacomo Dattolo
- Lia Crotti (ORCID: https://orcid.org/0000-0002-5728-3158)
- Maurizio Sguazzotti (ORCID: https://orcid.org/0009-0004-7063-345X)
- Chiara Calore
- Giacomo Tini (ORCID: https://orcid.org/0000-0001-8520-152X)
- Marco Canepa (ORCID: https://orcid.org/0000-0001-9063-5576)
- Francesca Fumero
- Elena Biagini (ORCID: https://orcid.org/0000-0003-0295-0440)
- Vladyslav Chubuchnyi
- Francesco Cappelli (ORCID: https://orcid.org/0000-0002-1622-0732)
- Andrea Igoren Guaricci (ORCID: https://orcid.org/0000-0001-7133-4401)
- Daniele Melis (ORCID: https://orcid.org/0000-0001-5871-2498)
- P Tofoni
- Maria Giulia Bellicini
- Federica Verrillo
- Paolo Bellocchi
- Federica Re (ORCID: https://orcid.org/0000-0003-2264-9428)
- Giuseppe Musumeci (ORCID: https://orcid.org/0000-0002-0306-1699)
- Marika Martini (ORCID: https://orcid.org/0009-0000-0522-8408)
- Gianfranco Sinagra
- Alberto Aimo
- Anna Maria Napoli
- Claudio Bergami
Institutions
- Università degli Studi del Piemonte Orientale “Amedeo Avogadro” (IT)
- University of Udine (IT)
- University of Padua (IT)
- University of Trieste (IT)
- Università degli studi di Cassino e del Lazio Meridionale (IT)
- University of Milan (IT)
- University of Campania "Luigi Vanvitelli" (IT)
- Fondazione IRCCS Ca' Granda Ospedale Maggiore Policlinico (IT)
- University of Catania (IT)
- Ospedale Maggiore (IT)
- Centro Cardiologico Monzino (IT)
- Fondazione Ricerca Molinette (IT)
- Surgical Specialties (Canada) (CA)
- Azienda Ospedaliero-Universitaria Careggi (IT)
- Azienda USL di Bologna (IT)
- Ospedale Santa Maria della Misericordia di Udine (IT)
- A. O. Ordine Mauriziano di Torino (IT)
- IRCCS Istituto Auxologico Italiano (IT)
- Nini Hospital (LB)
- ERN GUARD-Heart (NL)
- Istituti di Ricovero e Cura a Carattere Scientifico (IT)
- Piedmont University (US)
- Fondazione Toscana Gabriele Monasterio (IT)
- Azienda Sanitaria Universitaria Integrata di Trieste (IT)
- University of Bari Aldo Moro (IT)
- University of Milano-Bicocca (IT)
- University of Brescia (IT)
- University of Genoa (IT)
- Sapienza University of Rome (IT)
Publication Details
- Journal
- Journal of Cardiovascular Medicine
- Published
- 2025-06-20
- DOI
- https://doi.org/10.2459/jcm.0000000000001746
- Citations
- 1
- Primary Topic
- Cardiomyopathy and Myosin Studies
- Type
- article
- Field-Weighted Citation Impact
- 1.39