Patient experience with familial chylomicronemia syndrome before and after olezarsen treatment: Qualitative interviews with clinical trial participants
Results of this qualitative study underscore the significant burden of FCS and support the effectiveness of olezarsen from the patient perspective.
Authors
- Emily Bratlee‐Whitaker (ORCID: https://orcid.org/0000-0003-0582-9195)
- Montserrat Vera Llonch
- Sheri Fehnel (ORCID: https://orcid.org/0000-0001-8568-0102)
- Alexis Baass (ORCID: https://orcid.org/0000-0001-9534-1657)
- Asia Sikora Kessler (ORCID: https://orcid.org/0000-0001-9417-6637)
- Maurizio Averna (ORCID: https://orcid.org/0000-0003-3558-9209)
- Marcello Arca (ORCID: https://orcid.org/0000-0003-3786-0883)
- Veronica J. Alexander (ORCID: https://orcid.org/0000-0003-3729-5749)
- Seth J. Baum (ORCID: https://orcid.org/0000-0003-1202-8126)
- T. Michelle Brown (ORCID: https://orcid.org/0000-0002-4580-805X)
- Ovidio Muñiz-Grijalvo (ORCID: https://orcid.org/0000-0003-2230-6556)
- Daniel Gaudet (ORCID: https://orcid.org/0000-0002-5185-3666)
- Sotirios Tsimikas (ORCID: https://orcid.org/0000-0001-9834-9494)
- Jean Bergeron (ORCID: https://orcid.org/0000-0003-4007-8024)
Institutions
- Ionis Pharmaceuticals (United States) (US)
- Boca Raton Regional Hospital (US)
- Centre hospitalier universitaire de Québec (CA)
- RTI Health Solutions (US)
- Centre hospitalier de l'Université Laval (CA)
- Instituto di Biofisica (ES)
- Hospital Universitario Virgen del Rocío (ES)
- Istituto Nazionale di Fisica Nucleare, Sezione di Roma I (IT)
- Montreal Clinical Research Institute (CA)
- Université de Montréal (CA)
- Sapienza University of Rome (IT)
- University of Palermo (IT)
Publication Details
- Journal
- Journal of clinical lipidology
- Published
- 2025-06-18
- DOI
- https://doi.org/10.1016/j.jacl.2025.06.014
- Citations
- 1
- Primary Topic
- Lipid metabolism and disorders
- Type
- article
- Field-Weighted Citation Impact
- 1.39
Funders
- Ionis Pharmaceuticals