Athinoula A. Martinos Center for Biomedical Imaging, Massachusetts General Hospital
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article
Safety and efficacy of leriglitazone in childhood cerebral adrenoleukodystrophy (NEXUS): an interim analysis of an open-label, phase 2/3 trial
Hendrik Rosewich, Uwe Meya, Eric J. Mallack, Arun Mistry et al.
Citations
3 citations
Journal
EClinicalMedicine
Topics
Peroxisome Proliferator-Activated Receptors
Field-Weighted Citation Impact (FWCI)
2.42
article
Safety and efficacy of leriglitazone in childhood cerebral adrenoleukodystrophy (NEXUS): an interim analysis of an open-label, phase 2/3 trial
Hendrik Rosewich, Uwe Meya, Eric J. Mallack, Arun Mistry, Sílvia Pascual, Otto Rapalino, Pilar Pizcueta, Gloria Chia-Yi Chiang, Patricia L. Musolino, Adriana Mantilla, A. Vilà, Laura Rodríguez‐Pascau, Guillem Pina, Ángeles García‐Cazorla, Paul A. Caruso, Caroline Sevin, Marco Emanuele, Sandra Jimenez, M Rovira, M. Pascual, Marc Martinell, Elise Yazbeck, Karl G. Helmer, S. Bennett, Juliana Ribeiro Constante, Daniel Balentine
article en
3 citations
Abstract
No abstract available for this paper.
Publication Tag
EClinicalMedicineVol. 84
Institutions
Kennedy Krieger Institute (US), Hospital Sant Joan de Déu Barcelona (ES), NewYork–Presbyterian Hospital (US), Harvard University (US), Johns Hopkins University (US), Cornell University (US), Lenox Hill Hospital (US), New York Hospital Queens (US), German Center for Pediatric and Adolescent Rheumatology (DE), Massachusetts General Hospital (US), Presbyterian Hospital (US), Clinical Trial and Consulting (US), Hasbro Children's Hospital (US), Universitätsmedizin Göttingen (DE), Light Prescriptions Innovators (Spain) (ES), University Children's Hospital Tübingen (DE), Athinoula A. Martinos Center for Biomedical Imaging (US), Bicêtre Hospital (FR), University of Göttingen (DE)
Funders
Centre d'Imagerie BioMédicale, Athinoula A. Martinos Center for Biomedical Imaging, Massachusetts General Hospital