Eculizumab for Thrombotic Microangiopathy Induced by Onasemnogene Abeparvovec in Spinal Muscular Atrophy
Thrombotic microangiopathy is an ultra-rare, but potentially life-threatening condition that can occur after onasemnogene abeparvovec therapy. Anticipation of these serious adverse events, its prompt recognition and treatment is crucial for a better outcome.
Authors
- Tanja Kersnik Levart
- Damjan Osredkar (ORCID: https://orcid.org/0000-0002-2188-420X)
- Anja Troha Gergeli (ORCID: https://orcid.org/0000-0001-8075-3093)
- Nilamadhab Kar (ORCID: https://orcid.org/0000-0002-8801-9245)
- Tanja Loboda (ORCID: https://orcid.org/0000-0001-8689-6159)
- Eva Vrščaj (ORCID: https://orcid.org/0000-0002-1510-0501)
- Chiara Močnik Pegan
Institutions
- University of Ljubljana (SI)
- Ljubljana University Medical Centre (SI)
Publication Details
- Journal
- Case Reports in Nephrology and Dialysis
- Published
- 2025-05-23
- DOI
- https://doi.org/10.1159/000546114
- Primary Topic
- Neurogenetic and Muscular Disorders Research
- Type
- article
- Field-Weighted Citation Impact
- 0.00