Mapping the rare disease paediatric clinical trial availabilities in Europe

Heatmap analyses reveal a significant but incomplete overlap of RD clinical trial sites between ERNs and c4c in parts of Europe, suggesting strong potential for cross-network collaboration to enhance paediatric RD trial recruitment and outcomes.

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Publication Details

Journal
Frontiers in Pediatrics
Published
2025-05-19
DOI
https://doi.org/10.3389/fped.2025.1523847
Citations
1
Primary Topic
Genomics and Rare Diseases
Type
article
Field-Weighted Citation Impact
1.82
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article

Mapping the rare disease paediatric clinical trial availabilities in Europe

Ann Raes, Franz Schaefer, Johan Vande Walle, Eva Degraeuwe et al.
1 citations
Frontiers in Pediatrics
Genomics and Rare Diseases
1.82
article

Mapping the rare disease paediatric clinical trial availabilities in Europe

Ann Raes, Franz Schaefer, Johan Vande Walle, Eva Degraeuwe, Ricardo M. Fernandes, M. Turner
article en
1 citations

Abstract

Heatmap analyses reveal a significant but incomplete overlap of RD clinical trial sites between ERNs and c4c in parts of Europe, suggesting strong potential for cross-network collaboration to enhance paediatric RD trial recruitment and outcomes.

Frontiers in PediatricsVol. 13
University of Lisbon (PT), University of Liverpool (GB), Heidelberg University (DE), Ghent University Hospital (BE), University Hospital Heidelberg (DE), Ghent University (BE), ERN GUARD-Heart (NL)
Partnerships for the goals
Openalex Percentile: Top 16%
Genomics and Rare Diseases
1.82
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