Mapping the rare disease paediatric clinical trial availabilities in Europe
Heatmap analyses reveal a significant but incomplete overlap of RD clinical trial sites between ERNs and c4c in parts of Europe, suggesting strong potential for cross-network collaboration to enhance paediatric RD trial recruitment and outcomes.
Authors
- Ann Raes (ORCID: https://orcid.org/0000-0001-7809-2505)
- Franz Schaefer (ORCID: https://orcid.org/0000-0001-7564-9937)
- Johan Vande Walle (ORCID: https://orcid.org/0000-0001-9700-5358)
- Eva Degraeuwe (ORCID: https://orcid.org/0000-0003-2523-3022)
- Ricardo M. Fernandes (ORCID: https://orcid.org/0000-0002-7253-6475)
- M. Turner (ORCID: https://orcid.org/0000-0002-5299-8656)
Institutions
- University of Lisbon (PT)
- University of Liverpool (GB)
- Heidelberg University (DE)
- Ghent University Hospital (BE)
- University Hospital Heidelberg (DE)
- Ghent University (BE)
- ERN GUARD-Heart (NL)
Publication Details
- Journal
- Frontiers in Pediatrics
- Published
- 2025-05-19
- DOI
- https://doi.org/10.3389/fped.2025.1523847
- Citations
- 1
- Primary Topic
- Genomics and Rare Diseases
- Type
- article
- Field-Weighted Citation Impact
- 1.82