SMA Community Priorities for Future Drug Therapies: Cross-Sectional Survey Findings Representing 410 Adults with SMA
Authors
- Mary Ann Curry (ORCID: https://orcid.org/0000-0002-0747-4669)
- Ramaa Chitale (ORCID: https://orcid.org/0000-0002-0984-8433)
- Ilse Peterson (ORCID: https://orcid.org/0000-0001-6579-9720)
- Lisa Belter (ORCID: https://orcid.org/0000-0002-8348-1916)
Institutions
- Independent Sector (US)
- Cure Spinal Muscular Atrophy (US)
Publication Details
- Journal
- Neurology and Therapy
- Published
- 2025-05-03
- DOI
- https://doi.org/10.1007/s40120-025-00753-7
- Primary Topic
- Neurogenetic and Muscular Disorders Research
- Type
- article
- Field-Weighted Citation Impact
- 0.00