RAG-17, a Novel siRNA Therapy for SOD1-ALS: Safety and Preliminary Efficacy from a First-in-human Trial (S5.003)
Authors
- Xuejiao Zhou (ORCID: https://orcid.org/0000-0002-4613-3349)
- Hui Qu (ORCID: https://orcid.org/0000-0003-4809-570X)
- Long‐Cheng Li (ORCID: https://orcid.org/0000-0002-3971-6335)
- Xiaoling Liao (ORCID: https://orcid.org/0000-0003-4905-845X)
- Lingling Jiang (ORCID: https://orcid.org/0000-0002-3343-6279)
- Shawn Zhang
- Yuesong Pan (ORCID: https://orcid.org/0000-0003-3082-6789)
- Xuan Wang (ORCID: https://orcid.org/0000-0001-8487-6672)
- Ling Wang (ORCID: https://orcid.org/0000-0002-5129-4999)
- Yilong Wang (ORCID: https://orcid.org/0000-0003-2725-2788)
- Weiqi Chen (ORCID: https://orcid.org/0000-0002-2551-9314)
- Moorim Kang
- J Ye
Institutions
- Capital Medical University (CN)
- Beijing Tian Tan Hospital (CN)