RNAi-based Therapies for Hereditary Transthyretin Amyloidosis with Polyneuropathy: A Meta-analysis of Randomized Clinical Trials (P12-11.013)
This meta-analysis aims to evaluate the efficacy and safety of RNA inhibitor therapies in treating Hereditary transthyretin amyloidosis (hATTR) with polyneuropathy.
Authors
- Pedro Carneiro (ORCID: https://orcid.org/0000-0003-1699-6968)
- Luis T. Campos (ORCID: https://orcid.org/0009-0006-5465-6795)
- Paweł Łajczak (ORCID: https://orcid.org/0000-0003-0281-5417)
- Oguz Kagan Sahin (ORCID: https://orcid.org/0009-0006-0001-0390)
- Yasmin Silva (ORCID: https://orcid.org/0000-0002-4453-1829)
- Luana Makita
- Aishwarya Koppanatham (ORCID: https://orcid.org/0009-0000-5737-4474)
- Murilo Cruccioli
Institutions
- University of Debrecen (HU)
- Universidade de Ribeirão Preto (BR)
- Medical University of Silesia (PL)
- Acıbadem University (TR)
- Universidade de Santo Amaro (BR)
- Universidade Federal do Paraná (BR)
Publication Details
- Journal
- Neurology
- Published
- 2025-04-07
- DOI
- https://doi.org/10.1212/wnl.0000000000211351
- Primary Topic
- Amyloidosis: Diagnosis, Treatment, Outcomes
- Type
- article
- Field-Weighted Citation Impact
- 0.00