LEOPARD-DMD: Six-Month Results of Longitudinal Study of Disease Progression of Duchenne Muscular Dystrophy through the Patient and Caregiver Perspective (P7-6.007)
To conduct a remote, 2-year longitudinal study with individuals with DMD and caregivers of individuals with DMD to determine track disease burden over time and identify factors associated with a faster or slower progression of disease.
Authors
- Jennifer Weinstein (ORCID: https://orcid.org/0000-0002-3984-2120)
- Anika Varma (ORCID: https://orcid.org/0000-0001-9533-7113)
- Alicia Brocht
- Emma Ciafaloni (ORCID: https://orcid.org/0000-0002-3925-3289)
- Preshetha Kanagaiah (ORCID: https://orcid.org/0000-0002-4675-0910)
- Peggy Auinger (ORCID: https://orcid.org/0000-0002-5262-8946)
- Spencer Rosero (ORCID: https://orcid.org/0000-0001-9958-1172)
- Charlotte Engebrecht (ORCID: https://orcid.org/0009-0002-2982-8197)
- Debra Guntrum
- Chad Heatwole (ORCID: https://orcid.org/0000-0002-2900-6612)
- Christina Shupe
- Charlotte Irwin
- Judith Monickaraj
Institutions
- Spencer Foundation (US)
- University of Rochester Medical Center (US)
- University of Rochester (US)
Publication Details
- Journal
- Neurology
- Published
- 2025-04-07
- DOI
- https://doi.org/10.1212/wnl.0000000000212104
- Primary Topic
- Muscle Physiology and Disorders
- Type
- article
- Field-Weighted Citation Impact
- 0.00