Clinical Outcomes of Adult Spinal Muscular Atrophy Patients on Appropriate Pharmaceutical Interventions: A Retrospective Chart Review (P11-11.020)
To investigate the efficacy of intrathecal nusinersen and oral risdiplam on adults with spinal muscular atrophy (SMA).
Authors
- Christina Chrisman
- Dominic Julian (ORCID: https://orcid.org/0000-0001-7352-4997)
- James E. Bates (ORCID: https://orcid.org/0000-0001-7060-7156)
- James Kelbert (ORCID: https://orcid.org/0009-0008-2274-1412)
- Rachel Schuurs
Institutions
- University of Arizona (US)
- Banner - University Medical Center Phoenix (US)
Publication Details
- Journal
- Neurology
- Published
- 2025-04-07
- DOI
- https://doi.org/10.1212/wnl.0000000000212448
- Primary Topic
- Neurogenetic and Muscular Disorders Research
- Type
- article
- Field-Weighted Citation Impact
- 0.00