Clinical Outcomes of Adult Spinal Muscular Atrophy Patients on Appropriate Pharmaceutical Interventions: A Retrospective Chart Review (P11-11.020)

To investigate the efficacy of intrathecal nusinersen and oral risdiplam on adults with spinal muscular atrophy (SMA).

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Publication Details

Journal
Neurology
Published
2025-04-07
DOI
https://doi.org/10.1212/wnl.0000000000212448
Primary Topic
Neurogenetic and Muscular Disorders Research
Type
article
Field-Weighted Citation Impact
0.00
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article

Clinical Outcomes of Adult Spinal Muscular Atrophy Patients on Appropriate Pharmaceutical Interventions: A Retrospective Chart Review (P11-11.020)

Christina Chrisman, Dominic Julian, James E. Bates, James Kelbert et al.
Neurology
Neurogenetic and Muscular Disorders Research
article

Clinical Outcomes of Adult Spinal Muscular Atrophy Patients on Appropriate Pharmaceutical Interventions: A Retrospective Chart Review (P11-11.020)

Christina Chrisman, Dominic Julian, James E. Bates, James Kelbert, Rachel Schuurs
article en

Abstract

To investigate the efficacy of intrathecal nusinersen and oral risdiplam on adults with spinal muscular atrophy (SMA).

NeurologyVol. 104(7_Supplement_1)
University of Arizona (US), Banner - University Medical Center Phoenix (US)
Openalex Percentile: Top 90%
Neurogenetic and Muscular Disorders Research
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Clinical Outcomes of Adult Spinal Muscular Atrophy Patients on Appropriate Pharmaceutical Interventions: A Retrospective Chart Review (P11-11.020) — Christina Chrisman, Dominic Julian, et al. · Neurology (2025) | TGRS Research Map | TGRS