RNAi Therapeutics for hATTR Amyloidosis: A Comprehensive Single Arm Meta-Analysis of Clinical Outcomes and Treatment Efficacy (P9-2.005)
The primary objective of this single-arm meta-analysis is to comprehensively evaluate the efficacy and clinical outcomes of RNA interference (RNAi) therapies, specifically patisiran and vutrisiran, in the treatment of hereditary transthyretin amyloidosis (hATTR) with neurologic involvement.
Authors
- Alberto Múñoz (ORCID: https://orcid.org/0000-0003-3890-4251)
- Karolina Elizabeth Ante Ramírez
- A Briseño (ORCID: https://orcid.org/0009-0004-0360-6419)
- María Andrea Hernández-Castañeda (ORCID: https://orcid.org/0000-0002-7151-3546)
- César Serrano (ORCID: https://orcid.org/0000-0003-1416-8739)
- Marı́a Luisa Vargas (ORCID: https://orcid.org/0000-0002-4744-9986)
- Sergio Morales Acosta (ORCID: https://orcid.org/0009-0003-9237-4842)
- Jorge Vargas (ORCID: https://orcid.org/0009-0002-7738-245X)
- VC Romano
- B. Toledo del Castillo
Institutions
- Universidad Autónoma de Bucaramanga (CO)
- Universidad de Guadalajara (MX)
- Universidad Autónoma de Sinaloa (MX)
- Universidad UTE (EC)
- Fundación Universitaria de Ciencias de la Salud (CO)
- Universidad Cuauhtémoc (MX)
- Benemérita Universidad Autónoma de Puebla (MX)
Publication Details
- Journal
- Neurology
- Published
- 2025-04-07
- DOI
- https://doi.org/10.1212/wnl.0000000000211059
- Primary Topic
- Amyloidosis: Diagnosis, Treatment, Outcomes
- Type
- article
- Field-Weighted Citation Impact
- 0.00