Real-World Use of Fenfluramine for Dravet Syndrome: a Retrospective Cohort Study Using a National Pharmacy Database (P12-9.002)
This study describes mortality rates and real-world use of fenfluramine (FFA) in United States (US) patients with Dravet syndrome (DS) who were new FFA users, obtained from a single specialty pharmacy.
Authors
- Judith Helen Cross (ORCID: https://orcid.org/0000-0001-7345-4829)
- Orrin Devinsky (ORCID: https://orcid.org/0000-0003-0044-4632)
- Michael Rañopa
- Renzo Guerrini (ORCID: https://orcid.org/0000-0002-7272-7079)
- Wesley T. Kerr (ORCID: https://orcid.org/0000-0002-5546-5951)
- Sylvain Rheims (ORCID: https://orcid.org/0000-0002-4663-8515)
- Elizabeth Donner (ORCID: https://orcid.org/0000-0003-1126-0548)
- Jeffrey L. Noebels (ORCID: https://orcid.org/0000-0002-2887-0839)
- Philippe Ryvlin (ORCID: https://orcid.org/0000-0001-7775-6576)
- António Gil‐Nagel (ORCID: https://orcid.org/0000-0003-4515-0793)
- Ingrid Eileen Scheffer (ORCID: https://orcid.org/0000-0002-2311-2174)
- Jenna Roberts (ORCID: https://orcid.org/0000-0001-6959-3025)
- Samden D. Lhatoo (ORCID: https://orcid.org/0000-0001-8626-1137)
- Elaine C. Wirrell (ORCID: https://orcid.org/0000-0003-3015-8282)
- Lieven G. Lagae (ORCID: https://orcid.org/0000-0002-7118-0139)
- Amélie Lothe (ORCID: https://orcid.org/0009-0001-9337-054X)
- Joseph Sullivan (ORCID: https://orcid.org/0000-0003-2081-8988)
- Milena Tryfon
Institutions
- Université Claude Bernard Lyon 1 (FR)
- Royal Children's Hospital (AU)
- University of Pittsburgh (US)
- University of California, San Francisco (US)
- Baylor College of Medicine (US)
- University of Toronto (CA)
- Great Ormond Street Hospital (GB)
- Hospital for Sick Children (CA)
- NYU Langone Health (US)
- Hospices Civils de Lyon (FR)
- Meyer Children's Hospital (IL)
- Mayo Clinic in Arizona (US)
- UCSF Benioff Children's Hospital (US)
- SickKids Foundation (CA)
- ERN GUARD-Heart (NL)
- Murdoch Children's Research Institute (AU)
- Hospital Ruber Internacional (ES)
- University College London (GB)
- The University of Texas Health Science Center at Houston (US)
- University of Lausanne (CH)
- KU Leuven (BE)
Publication Details
- Journal
- Neurology
- Published
- 2025-04-07
- DOI
- https://doi.org/10.1212/wnl.0000000000210591
- Primary Topic
- Epilepsy research and treatment
- Type
- article
- Field-Weighted Citation Impact
- 0.00