Unleashing the Potential of Givinostat: A Novel Therapy for Duchenne Muscular Dystrophy
Givinostat represents a paradigm shift in DMD management, offering benefits beyond corticosteroids by reducing fibrosis and promoting muscle regeneration. While its long-term safety and cost-effectiveness require further evaluation, its combination potential with gene therapies highlights its importance in future DMD treatment strategies. Ongoing studies aim to refine its role in broader neuromuscular disorders.
Authors
- Ahmad Furqan Anjum (ORCID: https://orcid.org/0009-0005-9616-0969)
- Muhammad Burhan Anjum (ORCID: https://orcid.org/0000-0003-4112-5961)
- Raza Ur Rehman (ORCID: https://orcid.org/0009-0003-5173-5023)
Institutions
- Farooq Hospital (PK)
- Shaikh Zayed Postgraduate Medical Institute (PK)
Publication Details
- Journal
- Current Therapeutic Research
- Published
- 2025-01-01
- DOI
- https://doi.org/10.1016/j.curtheres.2025.100787
- Citations
- 4
- Primary Topic
- Muscle Physiology and Disorders
- Type
- article
- Field-Weighted Citation Impact
- 3.22