Administration practices of and adherence to nusinersen in children with spinal muscular atrophy: a multicenter disease registry study in China
Findings from the analysis demonstrated high real-world adherence to nusinersen in Chinese children with SMA.
Authors
- Hua Wang (ORCID: https://orcid.org/0000-0001-8396-809X)
- Shanshan Mao (ORCID: https://orcid.org/0000-0001-6736-1407)
- Xinguo Lu (ORCID: https://orcid.org/0000-0001-8452-7608)
- Liwen Wu (ORCID: https://orcid.org/0000-0003-1031-7899)
- Xiaoli Yao (ORCID: https://orcid.org/0000-0003-2613-7956)
- Ken Chen (ORCID: https://orcid.org/0000-0003-4013-5279)
- Li Zhang (ORCID: https://orcid.org/0000-0002-3617-2627)
- Rong Luo (ORCID: https://orcid.org/0000-0003-3982-8772)
- Jianmin Liang
- Xiuxia Wang (ORCID: https://orcid.org/0000-0003-2756-9144)
- Lin Yang (ORCID: https://orcid.org/0000-0002-7114-1842)
- Jing Peng (ORCID: https://orcid.org/0009-0002-3216-5144)
- Yanyan Xia
- Jianmin Zhong (ORCID: https://orcid.org/0000-0003-3203-6094)
- Ruifeng Jin
- Jun Hu
- Zhe Tao
- Siqi Hong
- Dan Sun
- Xiaoli Zhang (ORCID: https://orcid.org/0000-0002-6738-1122)
- Yi Wang (ORCID: https://orcid.org/0000-0001-9081-120X)
Institutions
- Hebei Medical University (CN)
- Fujian Medical University (CN)
- Central South University (CN)
- Shandong University (CN)
- Sun Yat-sen University (CN)
- Jilin University (CN)
- Sichuan University (CN)
- West China Second University Hospital of Sichuan University (CN)
- Ta Solutions (China) (CN)
- Second Hospital of Hebei Medical University (CN)
- Children's Hospital of Zhejiang University (CN)
- First Hospital of Jilin University (CN)
- The First Affiliated Hospital, Sun Yat-sen University (CN)
- Dalian Maternal and Child Health Hospital (CN)
- Second Affiliated Hospital of Xi'an Jiaotong University (CN)
- Hunan Children's Hospital (CN)
- Wuhan Children's Hospital (CN)
- Third Affiliated Hospital of Zhengzhou University (CN)
- Jiangxi Provincial Children's Hospital (CN)
- Shenzhen Children's Hospital (CN)
- Children's Hospital of Fudan University (CN)
- Children's Hospital of Chongqing Medical University (CN)
- Xiangya Hospital Central South University (CN)
- Union Hospital (CN)
- Huazhong University of Science and Technology (CN)
- Chongqing Medical University (CN)
- China Medical University (CN)
Publication Details
- Journal
- BMC Pediatrics
- Published
- 2025-03-27
- DOI
- https://doi.org/10.1186/s12887-024-05290-0
- Citations
- 5
- Primary Topic
- Neurogenetic and Muscular Disorders Research
- Type
- article
- Field-Weighted Citation Impact
- 8.13