Non malignant ACTH-Independent Cushing Syndrome in Pediatric Patients: A Retrospective Observational Cohort Study

ACTH-independent CS is rare but can lead to significant burden in children. Early diagnosis and management are essential. New drugs targeting adrenal steroid synthesis are awaited.

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Publication Details

Journal
Hormone Research in Paediatrics
Published
2025-03-25
DOI
https://doi.org/10.1159/000545265
Primary Topic
Bone Tumor Diagnosis and Treatments
Type
article
Field-Weighted Citation Impact
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article

Non malignant ACTH-Independent Cushing Syndrome in Pediatric Patients: A Retrospective Observational Cohort Study

Isabelle Flechtner, Laëtitia Martinerie, Laura González-Briceño, Marc Nicolino et al.
Hormone Research in Paediatrics
Bone Tumor Diagnosis and Treatments
article

Non malignant ACTH-Independent Cushing Syndrome in Pediatric Patients: A Retrospective Observational Cohort Study

Isabelle Flechtner, Laëtitia Martinerie, Laura González-Briceño, Marc Nicolino, María Beatriz Arrom Brañas, Athanasia Stoupa, Jerome Yves Bertherat, Magali Viaud, Adrien Nguyen Quoc, Caroline Storey, Sibylle Rovani, Dulanjalee Kariyawasam, Gaëlle Vermillac, Agnès Linglart, Dinane Samara‐Boustani, Caroline Thalassinos, Yamina Dassa, Alix Besançon, Michel Polak, Anya Rothenbühler, Thomas Blanc, Jacques Beltrand, Graziella Pinto, Virginie Ribault, M. Hassan
article en

Abstract

ACTH-independent CS is rare but can lead to significant burden in children. Early diagnosis and management are essential. New drugs targeting adrenal steroid synthesis are awaited.

Hormone Research in Paediatrics
Hôpital Necker-Enfants Malades (FR), Université Paris Cité (FR), Institut Necker Enfants Malades (FR), Hôpital Cochin (FR), Assistance Publique – Hôpitaux de Paris (FR), Hospices Civils de Lyon (FR), Hôpital Robert-Debré (FR), Bicêtre Hospital (FR), Université de Caen Normandie (FR)
Good health and well-being
Openalex Percentile: Top 91%
Bone Tumor Diagnosis and Treatments
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