Expanding the therapeutic role of highly purified cannabidiol in monogenic epilepsies: A multicenter real‐world study
This study supports CBD as a potential treatment for monogenic epilepsies beyond its licensed indications, demonstrating comparable effectiveness between approved and off-label use and suggesting genetic subgroups with promising treatment responses.
Authors
- Alia Ramírez-Camacho (ORCID: https://orcid.org/0000-0001-9720-8948)
- Luca Bergonzini (ORCID: https://orcid.org/0000-0001-8214-1816)
- Giulia Prato (ORCID: https://orcid.org/0000-0001-6634-2474)
- Francesca Bisulli (ORCID: https://orcid.org/0000-0002-1109-7296)
- Elena Gardella (ORCID: https://orcid.org/0000-0002-7138-6022)
- Domenica Battaglia (ORCID: https://orcid.org/0000-0003-0491-4021)
- Maria Margherita Mancardi (ORCID: https://orcid.org/0000-0001-5122-4029)
- Duccio Maria Cordelli (ORCID: https://orcid.org/0000-0002-1367-6419)
- Gabriela Reyes Valenzuela (ORCID: https://orcid.org/0000-0003-3849-4758)
- Ángel Aledo‐Serrano (ORCID: https://orcid.org/0000-0003-4889-3365)
- Jana Domínguez‐Carral (ORCID: https://orcid.org/0000-0002-7197-7391)
- Roberto Caraballo (ORCID: https://orcid.org/0000-0003-0259-1046)
- Emanuele Cerulli Irelli (ORCID: https://orcid.org/0000-0003-3906-555X)
- Andrea Rüegger (ORCID: https://orcid.org/0000-0001-9953-8457)
- Antonella Riva (ORCID: https://orcid.org/0000-0001-9152-5571)
- Georgia Ramantani (ORCID: https://orcid.org/0000-0002-7931-2327)
- Javier Peña‐Ceballos (ORCID: https://orcid.org/0000-0001-7260-1292)
- Patrick B. Moloney (ORCID: https://orcid.org/0000-0003-0997-2087)
- Alessandro Ascani Orsini (ORCID: https://orcid.org/0000-0001-5256-6573)
- Elisabetta Cesaroni (ORCID: https://orcid.org/0000-0002-7177-4500)
- Adolfo Mazzeo (ORCID: https://orcid.org/0000-0002-7014-6617)
- Marco Perulli (ORCID: https://orcid.org/0000-0003-3311-2765)
- Francesca Felicia Operto (ORCID: https://orcid.org/0000-0002-2444-8761)
- Valentina De Giorgis (ORCID: https://orcid.org/0000-0002-5828-7070)
- Antonietta Coppola (ORCID: https://orcid.org/0000-0002-4845-4293)
- Paolo Bonanni (ORCID: https://orcid.org/0000-0002-9448-9059)
- Laura Licchetta (ORCID: https://orcid.org/0000-0001-7979-9895)
- Sara Matricardi (ORCID: https://orcid.org/0000-0002-4403-6342)
- Carlo Di Bonaventura (ORCID: https://orcid.org/0000-0003-1890-5409)
- Pasquale Striano (ORCID: https://orcid.org/0000-0002-6065-1476)
- Carla Marini (ORCID: https://orcid.org/0000-0002-9212-2691)
- Giancarlo Di Gennaro (ORCID: https://orcid.org/0000-0003-3446-0788)
- Katarzyna Maria Mieszczanek
- Andrea Santangelo (ORCID: https://orcid.org/0000-0003-2668-6373)
- G Santangelo (ORCID: https://orcid.org/0009-0007-0813-6091)
- Alessandro Ferretti
- Marica Rubino
- Norman Delanty (ORCID: https://orcid.org/0000-0002-3953-9842)
- Susanna Casellato
Institutions
- University of Pisa (IT)
- Hospital Sant Joan de Déu Barcelona (ES)
- Royal College of Surgeons in Ireland (IE)
- University of Sassari (IT)
- University of Southern Denmark (DK)
- University of Pavia (IT)
- Garrahan Hospital (AR)
- Istituto Giannina Gaslini (IT)
- Beaumont Hospital (IE)
- Agostino Gemelli University Polyclinic (IT)
- Mater Misericordiae University Hospital (IE)
- Istituto Neurologico Mediterraneo (IT)
- University of Chieti-Pescara (IT)
- Azienda Ospedaliero Universitaria di Sassari (IT)
- CTO Andrea Alesini (IT)
- Istituto delle Scienze Neurologiche di Bologna (IT)
- University Children's Hospital Zurich (CH)
- Azienda di Rilievo Nazionale ed Alta Specializzazione (IT)
- IRCCS Eugenio Medea (IT)
- Istituti di Ricovero e Cura a Carattere Scientifico (IT)
- Institut de Recerca Sant Joan de Déu
- University of Naples Federico II (IT)
- University of Genoa (IT)
- Sapienza University of Rome (IT)
- University of Bologna (IT)
Publication Details
- Journal
- Epilepsia
- Published
- 2025-03-24
- DOI
- https://doi.org/10.1111/epi.18378
- Citations
- 9
- Primary Topic
- Cannabis and Cannabinoid Research
- Type
- article
- Field-Weighted Citation Impact
- 12.55