Kidney Outcomes in Patients With Hereditary Transthyretin Amyloid Nephropathy Treated With Transthyretin Stabilizers And Gene-Silencer Therapies
Our study highlights the underrecognized risk of chronic kidney disease (CKD) and end-stage kidney disease in ATTRv and suggests that siRNA could be a promising therapeutic option for the stabilization of kidney function.
Authors
- Cécile Cauquil
- Hamza Sakhi (ORCID: https://orcid.org/0000-0003-4977-2661)
- Noémie Jourde‐Chiche (ORCID: https://orcid.org/0000-0001-9315-1577)
- Anissa Moktefi (ORCID: https://orcid.org/0000-0002-6015-3979)
- Charlotte Mussini (ORCID: https://orcid.org/0009-0004-7759-2929)
- Albane Brodin-Sartorius
- Ilias Kounis (ORCID: https://orcid.org/0000-0002-9557-8838)
- Mohamad Zaidan (ORCID: https://orcid.org/0000-0002-6847-0821)
- Violaine Planté‐Bordeneuve (ORCID: https://orcid.org/0000-0002-7880-2316)
- Perrine Devic (ORCID: https://orcid.org/0000-0002-9010-1723)
- Mickaël Bobot (ORCID: https://orcid.org/0000-0002-9451-0372)
- Andoni Echaniz-Laguna
- Sarah Mouawad
- Justine Solignac (ORCID: https://orcid.org/0000-0002-3621-3329)
- Julien Dang (ORCID: https://orcid.org/0000-0002-5690-7424)
- Sophie Ferlicot (ORCID: https://orcid.org/0000-0003-4124-9227)
- Thibaud Damy (ORCID: https://orcid.org/0000-0003-4058-3848)
- Renaud Snanoudj (ORCID: https://orcid.org/0000-0002-6657-6235)
- Vincent Audard (ORCID: https://orcid.org/0000-0001-5343-2550)
- Céline Labeyrie (ORCID: https://orcid.org/0000-0001-9765-709X)
- Frank Bridoux (ORCID: https://orcid.org/0000-0002-2005-8424)
- Laurent Daniel (ORCID: https://orcid.org/0000-0002-7539-0109)
- Marie Essig (ORCID: https://orcid.org/0000-0002-2030-5616)
- Antoine Huart (ORCID: https://orcid.org/0009-0002-3898-8731)
- Delphine Campigli
Institutions
- Inserm (FR)
- Université de Versailles Saint-Quentin-en-Yvelines (FR)
- Assistance Publique – Hôpitaux de Paris (FR)
- Bicêtre Hospital (FR)
- Hôpital Paul-Brousse (FR)
Publication Details
- Journal
- Kidney International Reports
- Published
- 2025-03-24
- DOI
- https://doi.org/10.1016/j.ekir.2025.03.029
- Citations
- 2
- Primary Topic
- Amyloidosis: Diagnosis, Treatment, Outcomes
- Type
- article
- Field-Weighted Citation Impact
- 1.61