Allogeneic hematopoietic stem cell transplantation for mucopolysaccharidosis patients: a single-center experience and assessment of quality of life
HSCT is a good therapeutic option for MPS and improves the quality of life of patients. MPS patients with attenuated phenotypes provide a better outcome in ADL after HSCT.
Authors
- Yunting Lin (ORCID: https://orcid.org/0000-0001-8974-357X)
- Xiaoyuan Zhao (ORCID: https://orcid.org/0009-0009-2164-0510)
- Chunhua Zeng (ORCID: https://orcid.org/0000-0001-5954-1803)
- Minyan Jiang (ORCID: https://orcid.org/0000-0001-9101-9281)
- Sha liu
- Cuili Liang (ORCID: https://orcid.org/0000-0001-5350-4892)
- Yanna Cai (ORCID: https://orcid.org/0000-0001-8734-5949)
- Li Liu (ORCID: https://orcid.org/0000-0002-4330-5694)
- Wendong Zhang (ORCID: https://orcid.org/0000-0003-1762-9246)
- Yongxian Shao (ORCID: https://orcid.org/0000-0002-5413-224X)
- Huiying Sheng (ORCID: https://orcid.org/0000-0003-4726-9974)
- Hua Jiang (ORCID: https://orcid.org/0000-0002-7948-484X)
- Yonglan Huang (ORCID: https://orcid.org/0000-0002-7527-3754)
- Xueying Su
Institutions
- Guangzhou Women and Children Medical Center (CN)
- Guangzhou Medical University (CN)
Publication Details
- Journal
- The Italian Journal of Pediatrics/Italian journal of pediatrics
- Published
- 2025-03-18
- DOI
- https://doi.org/10.1186/s13052-025-01919-7
- Citations
- 4
- Primary Topic
- Lysosomal Storage Disorders Research
- Type
- article
- Field-Weighted Citation Impact
- 4.66
Funders
- Natural Science Foundation of Guangdong Province
- Guangdong Medical Research Foundation
- Guangzhou Institute of Pediatrics, Guangzhou Women and Childrens Medical Center
- Guangzhou Municipal Science and Technology Project