Clinical Evaluation of N‐Acetyl‐l‐Leucine in Niemann–Pick Disease Type C: A Critical Perspective

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Publication Details

Journal
Movement Disorders Clinical Practice
Published
2025-03-17
DOI
https://doi.org/10.1002/mdc3.70041
Primary Topic
Lysosomal Storage Disorders Research
Type
article
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article

Clinical Evaluation of N‐Acetyl‐l‐Leucine in Niemann–Pick Disease Type C: A Critical Perspective

Carla Holgado, Gala Lopez
Movement Disorders Clinical Practice
Lysosomal Storage Disorders Research
article

Clinical Evaluation of N‐Acetyl‐l‐Leucine in Niemann–Pick Disease Type C: A Critical Perspective

Carla Holgado, Gala Lopez
article en

Abstract

No abstract available for this paper.
Movement Disorders Clinical PracticeVol. 12(5)
Fundación para la Lucha contra las Enfermedades Neurológicas de la Infancia (AR)
Openalex Percentile: Top 94%
Lysosomal Storage Disorders Research
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Clinical Evaluation of N‐Acetyl‐l‐Leucine in Niemann–Pick Disease Type C: A Critical Perspective — Carla Holgado, Gala Lopez · Movement Disorders Clinical Practice (2025) | TGRS Research Map | TGRS