Real-world Outcome of Vosoritide Treatment in Children With Achondroplasia: A 12-month Retrospective Observational Study
In a real-world setting, children with ACH showed significant improvements in growth and physical function after 12 months of treatment with vosoritide.
Authors
- Susanna Reincke (ORCID: https://orcid.org/0000-0003-2286-5761)
- Mirko Rehberg (ORCID: https://orcid.org/0000-0001-9534-4102)
- Heike Hoyer‐Kuhn (ORCID: https://orcid.org/0000-0001-5297-3662)
- Oliver Semler (ORCID: https://orcid.org/0000-0003-0029-7556)
- Stefanie Stasek (ORCID: https://orcid.org/0009-0009-0195-9428)
- Eva Pfeiffer
- Shino Junghänel-Welzing
Institutions
- University of Cologne (DE)
- University Hospital Cologne (DE)
Publication Details
- Journal
- Journal of the Endocrine Society
- Published
- 2025-03-08
- DOI
- https://doi.org/10.1210/jendso/bvaf041
- Citations
- 9
- Primary Topic
- Connective tissue disorders research
- Type
- article
- Field-Weighted Citation Impact
- 16.36