Efficacy and safety of conventional disease-modifying antirheumatic drugs in VEXAS syndrome: real-world data from the international AIDA network
Many VEXAS patients report a partial benefit from cDMARDs, while a smaller yet not negligible number of patients exhibit a CR; cDMARDs remain a viable option for this disorder, especially when the initial GC dosage is low and the need for a steroid-sparing effect is not immediately urgent.
Authors
- Guillermo Ruiz‐Irastorza (ORCID: https://orcid.org/0000-0001-7788-1043)
- Monica Bocchia (ORCID: https://orcid.org/0000-0003-3538-3913)
- Gaafar Ragab (ORCID: https://orcid.org/0000-0001-6529-0334)
- Andrea Hinojosa‐Azaola (ORCID: https://orcid.org/0000-0002-4001-3995)
- Henrique Ayres Mayrink Giardini (ORCID: https://orcid.org/0000-0002-0860-0882)
- Florenzo Iannone (ORCID: https://orcid.org/0000-0003-0474-5344)
- Guillermo Arturo Guaracha-Basáñez (ORCID: https://orcid.org/0000-0001-8060-7301)
- Bruno Frediani (ORCID: https://orcid.org/0000-0001-6003-7567)
- Amato de Paulis (ORCID: https://orcid.org/0000-0003-0347-2540)
- Giuseppe Lopalco (ORCID: https://orcid.org/0000-0003-4524-9566)
- Carlomaurizio Montecucco (ORCID: https://orcid.org/0000-0001-8263-3925)
- Franco Franceschini (ORCID: https://orcid.org/0000-0003-3678-6124)
- Valeria Caggiano (ORCID: https://orcid.org/0000-0002-9907-4856)
- Antonio Vitale (ORCID: https://orcid.org/0000-0003-4469-7332)
- Paola Triggianese (ORCID: https://orcid.org/0000-0002-1954-2825)
- Ombretta Viapiana (ORCID: https://orcid.org/0000-0003-1917-5655)
- Lorenzo Dagna (ORCID: https://orcid.org/0000-0002-7428-315X)
- Abdurrahman Tufan (ORCID: https://orcid.org/0000-0001-6244-9362)
- Matteo Piga (ORCID: https://orcid.org/0000-0002-1126-8315)
- Chiara Baggio (ORCID: https://orcid.org/0009-0009-2862-8055)
- Paolo Sfriso (ORCID: https://orcid.org/0000-0001-6432-7174)
- Francesca Crisafulli (ORCID: https://orcid.org/0000-0003-0319-1538)
- Alessandro Tomelleri (ORCID: https://orcid.org/0000-0002-5440-2078)
- Alberto Cauli (ORCID: https://orcid.org/0000-0002-7955-6786)
- Alberto Balistreri (ORCID: https://orcid.org/0000-0002-7349-9725)
- Sara Bindoli (ORCID: https://orcid.org/0000-0002-9409-3329)
- Corrado Campochiaro (ORCID: https://orcid.org/0000-0001-6806-3794)
- Adriana Soto-Peleteiro (ORCID: https://orcid.org/0000-0001-8959-8683)
- Karina Jahnz‐Różyk (ORCID: https://orcid.org/0000-0002-3505-1858)
- José Hernández‐Rodríguez (ORCID: https://orcid.org/0000-0002-2357-2015)
- Ewa Więsik–Szewczyk (ORCID: https://orcid.org/0000-0001-8509-4453)
- Francesca Leone (ORCID: https://orcid.org/0009-0001-6640-8290)
- Luca Cantarini (ORCID: https://orcid.org/0000-0002-7352-1275)
- Francesco La Torre (ORCID: https://orcid.org/0000-0002-5235-2900)
- Perla Ayumi Kawakami‐Campos
- Carmelo Gurnari (ORCID: https://orcid.org/0000-0001-6829-5544)
- İbrahim Vasi (ORCID: https://orcid.org/0000-0003-1900-5752)
- Verónica Gómez‐Caverzaschi (ORCID: https://orcid.org/0000-0001-5242-6925)
- Edoardo Conticini (ORCID: https://orcid.org/0000-0002-3974-6606)
- Eduardo Martín‐Nares (ORCID: https://orcid.org/0000-0002-7911-1269)
- Alejandra de‐la‐Torre (ORCID: https://orcid.org/0000-0003-0684-1989)
- Andrés González García (ORCID: https://orcid.org/0000-0002-7367-9523)
- Riccardo Bixio (ORCID: https://orcid.org/0000-0001-9335-3371)
- Alicia Callisto (ORCID: https://orcid.org/0000-0002-3639-3040)
- Francesco Gavioli
- Jiram Torres‐Ruiz (ORCID: https://orcid.org/0000-0002-7882-1488)
- Sara M. Monti (ORCID: https://orcid.org/0000-0002-1800-6772)
- Mark Beecher (ORCID: https://orcid.org/0000-0003-0381-2744)
- Ilaria Mormile (ORCID: https://orcid.org/0000-0001-7599-5426)
- Rosetta Vitetta
- Pravin Hissaria (ORCID: https://orcid.org/0000-0002-0663-6312)
- Micol Frassi
- Jurgen Sota (ORCID: https://orcid.org/0000-0002-7549-2922)
- Olga Araújo (ORCID: https://orcid.org/0000-0003-1763-1880)
- Rafael Alves Cordeiro (ORCID: https://orcid.org/0000-0002-5695-9136)
- Ezgi Deniz Batu (ORCID: https://orcid.org/0000-0003-1065-2363)
- Claudia Fabiani (ORCID: https://orcid.org/0000-0003-4515-7741)
- Maria Antonietta D’Agostino
- Jessica Sbalchiero
- Mercedes Peña-Rodríguez
Institutions
- University of Siena (IT)
- Università Cattolica del Sacro Cuore (IT)
- South Australia Pathology (AU)
- University of Rome Tor Vergata (IT)
- Cleveland Clinic (US)
- Royal Adelaide Hospital (AU)
- University of Padua (IT)
- Cairo University (EG)
- Vita-Salute San Raffaele University (IT)
- University of the Basque Country (ES)
- University of Cagliari (IT)
- University of Pavia (IT)
- BioCruces Health research Institute (ES)
- Azienda Ospedaliera Universitaria Integrata Verona (IT)
- Instituto Nacional de Ciencias Médicas y Nutrición Salvador Zubirán (MX)
- CTO Andrea Alesini (IT)
- Instituto Ramón y Cajal de Investigación Sanitaria (ES)
- IRCCS Ospedale San Raffaele (IT)
- Azienda Ospedaliera Universitaria Senese (IT)
- Policlinico Tor Vergata (IT)
- Central Clinical Hospital (PL)
- Ospedale Pediatrico Giovanni XXIII (IT)
- Hospital das Clínicas da Faculdade de Medicina da Universidade de São Paulo (BR)
- Istituti di Ricovero e Cura a Carattere Scientifico (IT)
- Consorci Institut D'Investigacions Biomediques August Pi I Sunyer (ES)
- Hospital Universitario Ramón y Cajal (ES)
- University of Bari Aldo Moro (IT)
- Hacettepe University (TR)
- University of Naples Federico II (IT)
- Universitat de Barcelona (ES)
- University of Brescia (IT)
- Universidad del Rosario (CO)
- Gazi University (TR)
Publication Details
- Journal
- Frontiers in Pharmacology
- Published
- 2025-03-07
- DOI
- https://doi.org/10.3389/fphar.2025.1539756
- Citations
- 6
- Primary Topic
- Otitis Media and Relapsing Polychondritis
- Type
- article
- Field-Weighted Citation Impact
- 10.01
Funders
- Università degli Studi di Siena