First-in-human clinical study of an embryonic stem cell product for urea cycle disorders Authors Takako Yoshioka (ORCID: https://orcid.org/0000-0002-2644-1846) Reiko Horikawa (ORCID: https://orcid.org/0000-0003-3429-3246) Seisuke Sakamoto Yoshikazu Ito (ORCID: https://orcid.org/0000-0003-3322-6922) Kengo Sasaki (ORCID: https://orcid.org/0000-0002-3244-2845) Masashi Toyoda (ORCID: https://orcid.org/0000-0002-9432-6401) Shoko Miyajima Kazuhiko Nakabayashi (ORCID: https://orcid.org/0000-0003-2927-0963) Akihiro Umezawa (ORCID: https://orcid.org/0000-0002-0485-6653) Takashi Ohkura (ORCID: https://orcid.org/0000-0001-7951-647X) Saeko Akiyama (ORCID: https://orcid.org/0000-0002-5795-4302) Itaru Hayakawa (ORCID: https://orcid.org/0000-0002-6384-0205) Mureo Kasahara (ORCID: https://orcid.org/0000-0002-1651-0430) Shoko Miyata Akinari Fukuda (ORCID: https://orcid.org/0000-0003-4684-0446) Hidenori Akutsu Hajime Uchida (ORCID: https://orcid.org/0000-0002-7692-0095) Toshimasa Nakao (ORCID: https://orcid.org/0000-0003-1003-6800) Tasuku Kodama Shin Enosawa (ORCID: https://orcid.org/0000-0002-0818-8998) Yusuke Yanagi Osamu Miyazaki (ORCID: https://orcid.org/0000-0002-1793-4892) Palaksha Kanive Javaregowda (ORCID: https://orcid.org/0000-0002-5088-5391) Noriaki Saku Masakazu Machida Yasuyuki Fukuhara (ORCID: https://orcid.org/0000-0002-4081-6739) Shunsuke Nosaka (ORCID: https://orcid.org/0000-0002-9182-2717) Chizuko Okamatsu-Haga Yoshie Oishi Mayu Yamazaki‐Inoue Kenta Ite Naoko Nakamura (ORCID: https://orcid.org/0000-0002-3110-8159) Seiichi Shimizu (ORCID: https://orcid.org/0000-0002-6985-945X) Kazuaki Nakamura (ORCID: https://orcid.org/0000-0003-4999-5056) Takashi Igarashi (ORCID: https://orcid.org/0009-0001-7090-5505) Yoichi Matsubara (ORCID: https://orcid.org/0000-0001-5990-8214) Hidenori Nonaka (ORCID: https://orcid.org/0000-0002-4705-7587) Akira Masuda Rie Abutani-Sakamoto Institutions Tohoku University (JP) Sri Dharmasthala Manjunatheshwara College of Dental Sciences & Hospital (IN) National Center For Child Health and Development (JP) Publication Details Journal Stem Cell Research & Therapy Published 2025-03-06 DOI https://doi.org/10.1186/s13287-025-04162-3 Citations 7 Primary Topic Pluripotent Stem Cells Research Type article Field-Weighted Citation Impact 5.64 Funders Japan Agency for Medical Research and Development Japan Science and Technology Agency Explore the Global Research Space Interactive Map