Considerations for Regulatory Reusability of Dynamic Tools in the New Drug Development

Model-informed drug development (MIDD) approaches have become indispensable for new drug development and to address regulatory challenges. Dynamic tools, such as population pharmacokinetics (popPK), physiologically-based pharmacokinetics (PBPK), and quantitative systems pharmacology (QSP) models, are routinely employed to enhance the efficiency of drug development. Recently, the Fit-for-Purpose (FFP) initiative and the Model Master File (MMF) framework have emerged to support model reusability and sharing in regulatory settings. In this manuscript we share key insights from the Session "Pathways for Regulatory Acceptance of Dynamic Tools in the New Drug Space" of Workshop "Considerations and Potential Regulatory Applications for a Model Master File", hosted by the U.S. Food and Drug Administration (FDA) and the Center for Research on Complex Generics (CRCG) and discuss the considerations for regulatory acceptance of dynamic modeling tools. Presentations at the workshop explored current practices in PBPK model evaluation, the potential for popPK models in bioequivalence (BE) assessments, and the implications of reusing models. Challenges such as context-specific validation, version control, and the impact of scientific and technological advancements on model reuse were emphasized. The workshop underscored the importance of clear regulatory pathways and structured frameworks for the consistent application of reusable models. The MMF's potential to streamline reviews and reduce redundancies was noted, although operational details require further elaboration. Continued collaboration among stakeholders is essential to refine model-sharing practices, enhance model validation processes, and promote transparency, ensuring that MIDD approaches remain robust and adaptable to evolving regulatory needs.

Authors

Institutions

Publication Details

Journal
Pharmaceutical Research
Published
2025-03-04
DOI
https://doi.org/10.1007/s11095-025-03831-5
Citations
3
Primary Topic
Statistical Methods in Clinical Trials
Type
article
Field-Weighted Citation Impact
7.89
Controls
|||
ALL TIME
JAN
FEB
MAR
APR
MAY
JUN
JUL
AUG
SEP
OCT
article

Considerations for Regulatory Reusability of Dynamic Tools in the New Drug Development

Rajanikanth Madabushi, Yuching Yang, Liang Zhao, Cynthia J. Musante et al.
3 citations
Pharmaceutical Research
Statistical Methods in Clinical Trials
7.89
article

Considerations for Regulatory Reusability of Dynamic Tools in the New Drug Development

Rajanikanth Madabushi, Yuching Yang, Liang Zhao, Cynthia J. Musante, Jogarao Gobburu, Hao Zhu, Martin Klein, Jiang Liu
article en
3 citations

Abstract

Model-informed drug development (MIDD) approaches have become indispensable for new drug development and to address regulatory challenges. Dynamic tools, such as population pharmacokinetics (popPK), physiologically-based pharmacokinetics (PBPK), and quantitative systems pharmacology (QSP) models, are routinely employed to enhance the efficiency of drug development. Recently, the Fit-for-Purpose (FFP) initiative and the Model Master File (MMF) framework have emerged to support model reusability and sharing in regulatory settings. In this manuscript we share key insights from the Session "Pathways for Regulatory Acceptance of Dynamic Tools in the New Drug Space" of Workshop "Considerations and Potential Regulatory Applications for a Model Master File", hosted by the U.S. Food and Drug Administration (FDA) and the Center for Research on Complex Generics (CRCG) and discuss the considerations for regulatory acceptance of dynamic modeling tools. Presentations at the workshop explored current practices in PBPK model evaluation, the potential for popPK models in bioequivalence (BE) assessments, and the implications of reusing models. Challenges such as context-specific validation, version control, and the impact of scientific and technological advancements on model reuse were emphasized. The workshop underscored the importance of clear regulatory pathways and structured frameworks for the consistent application of reusable models. The MMF's potential to streamline reviews and reduce redundancies was noted, although operational details require further elaboration. Continued collaboration among stakeholders is essential to refine model-sharing practices, enhance model validation processes, and promote transparency, ensuring that MIDD approaches remain robust and adaptable to evolving regulatory needs.

Pharmaceutical ResearchVol. 42(5)
University of Maryland, Baltimore (US), Center for Drug Evaluation and Research (US), Pfizer (United States) (US), Quantitative BioSciences (US), University of Baltimore (US)
Partnerships for the goals
Openalex Percentile: Top 3%
Statistical Methods in Clinical Trials
7.89
AI Navigator

Ask Laika to Summarize, Analyze, and Connect papers live on the map.

Summarize Papers & Methodologies

Extract key findings, datasets, and comparative methods across publications.

Benchmark Rankings & Visual Analytics

Rank top research institutions, authors, funders, topics, and journals by Field-Weighted Citation Impact (FWCI) and paper volume with instant charts.

Connect Distant Disciplines

Bridge topological clusters on the map to find hidden collaborative intersections.