Navigating challenges and opportunities in orphan medicines: A spotlight commentary on rare diseases
Authors
- Dinko Vitezić (ORCID: https://orcid.org/0000-0002-6295-6580)
- Robert Likić (ORCID: https://orcid.org/0000-0003-1413-4862)
- Andrej Belančić (ORCID: https://orcid.org/0000-0001-7848-6600)
- Elvira Meni Maria Gkrinia (ORCID: https://orcid.org/0009-0002-1255-8653)
Institutions
- University Hospital Centre Zagreb (HR)
- University of Rijeka (HR)
- University of Zagreb (HR)
Publication Details
- Journal
- British Journal of Clinical Pharmacology
- Published
- 2025-02-16
- DOI
- https://doi.org/10.1002/bcp.70013
- Citations
- 7
- Primary Topic
- Genomics and Rare Diseases
- Type
- article
- Field-Weighted Citation Impact
- 12.72