Observational study of changes to glucocorticosteroid prescribing patterns in duchenne muscular dystrophy in the UK over the last decade
The use of deflazacort and daily regimes has steadily increased across the UK North Star Network in the last decade. This study provides one of the largest up-to-date real-world set of data of evolution in prescription patterns and the occurrence of side-effects in different groups of GC-treated DMD.
Authors
- Georgia Stimpson (ORCID: https://orcid.org/0000-0003-2795-9898)
- Michela Guglieri (ORCID: https://orcid.org/0000-0002-8455-0637)
- Giovanni Baranello (ORCID: https://orcid.org/0000-0003-4871-6692)
- Gregory Landon
- Anna Sárközy (ORCID: https://orcid.org/0000-0002-1353-0583)
- Francesco Muntoni (ORCID: https://orcid.org/0000-0002-9102-5232)
- Adnan Y. Manzur
Institutions
- Great Ormond Street Hospital (GB)
- Great Ormond Street Hospital for Children NHS Foundation Trust (GB)
- Newcastle upon Tyne Hospitals NHS Foundation Trust (GB)
- University College London (GB)
- Newcastle University (GB)
Publication Details
- Journal
- Journal of Neurology Neurosurgery & Psychiatry
- Published
- 2025-02-12
- DOI
- https://doi.org/10.1136/jnnp-2024-335223
- Citations
- 2
- Primary Topic
- Muscle Physiology and Disorders
- Type
- article
- Field-Weighted Citation Impact
- 1.61