Operationalising a Haemophilia Gene Editing Lexicon for Practical Use
A gene editing lexicon shows promise for improving the understanding of gene editing for all stakeholders in the haemophilia community. Ensuring the lexicon remains up to date with current therapies and appropriate strategies for adoption such as infographics will enable this resource to have maximum impact.
Authors
- William McKeown (ORCID: https://orcid.org/0009-0006-1916-041X)
- Cedric R.J.R. Hermans (ORCID: https://orcid.org/0000-0001-5429-8437)
- David E. Gutstein (ORCID: https://orcid.org/0000-0001-7776-3477)
- Steven W. Pipe (ORCID: https://orcid.org/0000-0003-2558-2089)
- Mark A. Kay (ORCID: https://orcid.org/0000-0002-2799-2615)
- Craig M. Kessler (ORCID: https://orcid.org/0000-0003-0599-5724)
- Paul Smith (ORCID: https://orcid.org/0000-0002-7850-8440)
- Flora Peyvandi (ORCID: https://orcid.org/0000-0001-7423-9864)
- Leonard A. Valentino (ORCID: https://orcid.org/0000-0002-7927-6418)
- Carmen Unzu (ORCID: https://orcid.org/0000-0002-1582-7196)
- Kate Khair (ORCID: https://orcid.org/0000-0003-2001-5958)
- Glenn F. Pierce (ORCID: https://orcid.org/0000-0002-3310-328X)
- Wolfgang Miesbach (ORCID: https://orcid.org/0000-0002-4506-0061)
- Virginie Delwart
- Micheala Jones
- Monisha Pillai
- Anil Sindhurakar
Institutions
- Goethe University Frankfurt (DE)
- Cliniques Universitaires Saint-Luc (BE)
- Georgetown University (US)
- Regeneron (United States) (US)
- University of Milan (IT)
- Canadian Hemophilia Society (CA)
- Antrim Area Hospital (GB)
- Michigan Medicine (US)
- University Hospital Frankfurt (DE)
- Human Gene Therapy Research Institute (US)
- Rush University (US)
- Universidad de Navarra (ES)
- Stanford University (US)
Publication Details
- Journal
- Haemophilia
- Published
- 2025-01-27
- DOI
- https://doi.org/10.1111/hae.15155
- Citations
- 1
- Primary Topic
- Hemophilia Treatment and Research
- Type
- article
- Field-Weighted Citation Impact
- 1.77
Funders
- Regeneron Pharmaceuticals