Reverse transcriptase inhibitors in Aicardi‐Goutières syndrome: Design and regulatory challenges in clinical trials for rare disease
This commentary is on the original article by Crow et al. on pages 750–757 of this issue.
Authors
- Russell C. Dale (ORCID: https://orcid.org/0000-0002-2495-1826)
Institutions
- The University of Sydney (AU)
- Children's Hospital at Westmead (AU)
Publication Details
- Journal
- Developmental Medicine & Child Neurology
- Published
- 2025-01-10
- DOI
- https://doi.org/10.1111/dmcn.16237
- Primary Topic
- interferon and immune responses
- Type
- article
- Field-Weighted Citation Impact
- 0.00