Development of a value assessment framework for Health Technology Assessment in rare diseases drugs: insights from a Delphi study in Brazil
A value assessment framework validated by key stakeholders of rare diseases in Brazil could contribute to improve HTA transparency, decision making, and efficiency of the healthcare system, and inspire the development of a local guidance for rare-disease HTA.
Authors
- Tatiane Bomfim Ribeiro (ORCID: https://orcid.org/0000-0003-4434-748X)
- Patrícia Melo Aguiar (ORCID: https://orcid.org/0000-0002-3957-4533)
- Luiza Vasconcelos Biglia (ORCID: https://orcid.org/0000-0003-1403-4167)
- Tácio de Mendonça Lima (ORCID: https://orcid.org/0000-0003-4395-2098)
- Arturo Felippini
Institutions
- Universidade Federal Fluminense (BR)
- Universidade de São Paulo (BR)
- Instituto Butantan (BR)
- Instituto Federal Fluminense (BR)
- Faculty of Public Health (GB)
Publication Details
- Journal
- International Journal of Technology Assessment in Health Care
- Published
- 2025-01-01
- DOI
- https://doi.org/10.1017/s0266462324004835
- Citations
- 5
- Primary Topic
- Health Systems, Economic Evaluations, Quality of Life
- Type
- article
- Field-Weighted Citation Impact
- 15.66