Comparative efficacy of risdiplam and nusinersen in Type 2 and 3 spinal muscular atrophy patients: A cohort study using real-world data
This study showed that both medications significantly changed the HFSME and RULM after 3 and 6 months of follow-up. However, there was no significant difference between the two drugs according to the HFSME.
Authors
- Morteza Heidari (ORCID: https://orcid.org/0000-0002-7487-569X)
- Hadi Montazerlotfelahi
- Gholamreza Zamani Ghaletaki
- Narjes Jafari (ORCID: https://orcid.org/0000-0002-7423-3814)
- Ali Akbar Momen (ORCID: https://orcid.org/0000-0001-9664-801X)
- Seyed Saeed Hashemi Nazari (ORCID: https://orcid.org/0000-0002-0883-3408)
- Mehran Beiraghi Toosi (ORCID: https://orcid.org/0000-0002-0569-1117)
- Ali Khajeh (ORCID: https://orcid.org/0000-0003-2146-9345)
- Marzieh Babaee
- Sara Memarian (ORCID: https://orcid.org/0000-0002-3534-0094)
- Shahriar Nafissi (ORCID: https://orcid.org/0000-0003-4763-4310)
- Mahmoud Reza Ashrafi (ORCID: https://orcid.org/0000-0001-5483-6549)
- Mohsen Mollamohammadi
- Alireza Abdi (ORCID: https://orcid.org/0000-0002-3184-2564)
- Hassan Bakhtiary (ORCID: https://orcid.org/0000-0003-4629-5193)
- Hossein Farshadmoghadam (ORCID: https://orcid.org/0000-0002-9812-1083)
- Farzad Fatehi (ORCID: https://orcid.org/0000-0002-6774-7825)
- Azita Tavasoli (ORCID: https://orcid.org/0000-0002-9215-7077)
- Bentolhoda Ziaadini (ORCID: https://orcid.org/0000-0003-4312-6060)
- Soroor Inaloo (ORCID: https://orcid.org/0000-0002-5621-3473)
- Masood Ghahvechi Akbari (ORCID: https://orcid.org/0000-0001-6319-8729)
- Mohammad Mehdi Nasehi (ORCID: https://orcid.org/0000-0003-3000-0637)
- Reza Shervin Badv (ORCID: https://orcid.org/0000-0002-7477-4688)
- Vahid Aminzadeh (ORCID: https://orcid.org/0000-0002-7612-8604)
- Sedighe Nikbakht
- Seyed Ahmad Hosseini (ORCID: https://orcid.org/0000-0001-6191-682X)
- Meisam Babaei (ORCID: https://orcid.org/0000-0002-5477-8200)
- Ramin Heshmat
- Mohammad Barzegar (ORCID: https://orcid.org/0009-0002-4227-3878)
- Mohammadreza Ghazavi
- Fakhreddin Shariatmadari
- Mohammad Mehdi Taghdiri
- Ali Abbaskhanian
- Seyyed Mohammad Mahdi Hosseiny
Institutions
- Hamedan University of Medical Sciences (IR)
- Isfahan University of Medical Sciences (IR)
- Zanjan University of Medical Sciences (IR)
- Ahvaz Jundishapur University of Medical Sciences (IR)
- Arak University of Medical Sciences (IR)
- Iran University of Medical Sciences (IR)
- Tabriz University of Medical Sciences (IR)
- Mashhad University of Medical Sciences (IR)
- Shiraz University of Medical Sciences (IR)
- Guilan University of Medical Sciences (IR)
- Kerman University of Medical Sciences (IR)
- Lorestan University of Medical Sciences (IR)
- Urmia University (IR)
- Sina Hospital (IR)
- Children's Medical Center (IR)
- Golestan University of Medical Sciences (IR)
- Stem Cell Technology Research Center (IR)
- Zahedan University of Medical Sciences (IR)
- North Khorasan University of Medical Sciences (IR)
- Alborz University of Medical Sciences (IR)
- Urmia University of Medical Sciences (IR)
- Shahid Beheshti University of Medical Sciences (IR)
- Qom University of Medical Science and Health Services (IR)
- Qazvin University of Medical Sciences (IR)
- Tehran University of Medical Sciences (IR)
- Mazandaran University of Medical Sciences (IR)
Publication Details
- Journal
- Journal of Neuromuscular Diseases
- Published
- 2024-11-01
- DOI
- https://doi.org/10.1177/22143602241288087
- Citations
- 7
- Primary Topic
- Neurogenetic and Muscular Disorders Research
- Type
- article
- Field-Weighted Citation Impact
- 3.07