The CMS Sickle Cell Gene Therapy Access Model
This Viewpoint explores and provides policy recommendations for the Cell and Gene Therapy Access Model recently launched by the US Centers for Medicare & Medicaid Services (CMS), which aims to increase access to Medicaid recipiencts with rare and severe diseases.
Authors
- Jeromie Ballreich (ORCID: https://orcid.org/0000-0003-2564-4577)
- Mariana P. Socal (ORCID: https://orcid.org/0000-0001-9459-4898)
- Ilina C. Odouard (ORCID: https://orcid.org/0009-0006-5431-3979)
Institutions
- Johns Hopkins University (US)
Publication Details
- Journal
- JAMA Pediatrics
- Published
- 2024-12-16
- DOI
- https://doi.org/10.1001/jamapediatrics.2024.5536
- Citations
- 8
- Primary Topic
- Hemoglobinopathies and Related Disorders
- Type
- article
- Field-Weighted Citation Impact
- 3.50