Expert consensus for the management of patients with achondroplasia in treatment with vosoritide

This protocol for the administration of vosoritide will allow standardised implementation and optimization of treatment outcomes. It also offers an opportunity to improve the management of achondroplasia in Spain through a comprehensive and interdisciplinary approach.

Authors

Institutions

Publication Details

Journal
Anales de Pediatría (English Edition)
Published
2024-12-01
DOI
https://doi.org/10.1016/j.anpede.2024.09.012
Citations
1
Primary Topic
Connective tissue disorders research
Type
article
Field-Weighted Citation Impact
0.55

Funders

Controls
|||
ALL TIME
JAN
FEB
MAR
APR
MAY
JUN
JUL
AUG
SEP
OCT
article

Expert consensus for the management of patients with achondroplasia in treatment with vosoritide

José Manuel Rodríguez Domingo, Isolina Riaño Galán, Ana Coral Barreda Bonis, Isabel Leiva‐Gea et al.
1 citations
Anales de Pediatría (English Edition)
Connective tissue disorders research
0.55
article

Expert consensus for the management of patients with achondroplasia in treatment with vosoritide

José Manuel Rodríguez Domingo, Isolina Riaño Galán, Ana Coral Barreda Bonis, Isabel Leiva‐Gea, Enrique Galán‐Gómez, Encarna Guillén‐Navarro
article en
1 citations

Abstract

This protocol for the administration of vosoritide will allow standardised implementation and optimization of treatment outcomes. It also offers an opportunity to improve the management of achondroplasia in Spain through a comprehensive and interdisciplinary approach.

Anales de Pediatría (English Edition)Vol. 101(6)
Universidad de Oviedo (ES), Hospital Universitario La Paz (ES), Hospital Regional Universitario de Málaga (ES), Unidad de Cirugía Artroscópica (ES), Centro de Implantología Cirugía Oral y Maxilofacial (ES), Instituto Murciano de Investigación Biosanitaria (ES), Instituto de Investigación Biomédica de Málaga (ES), Instituto de Investigación Sanitaria del Principado de Asturias (ES)
BioMarin Pharmaceutical
Good health and well-being
Openalex Percentile: Top 24%
Connective tissue disorders research
0.55
AI Navigator

Ask Laika to Summarize, Analyze, and Connect papers live on the map.

Summarize Papers & Methodologies

Extract key findings, datasets, and comparative methods across publications.

Benchmark Rankings & Visual Analytics

Rank top research institutions, authors, funders, topics, and journals by Field-Weighted Citation Impact (FWCI) and paper volume with instant charts.

Connect Distant Disciplines

Bridge topological clusters on the map to find hidden collaborative intersections.