Expert consensus for the management of patients with achondroplasia in treatment with vosoritide
This protocol for the administration of vosoritide will allow standardised implementation and optimization of treatment outcomes. It also offers an opportunity to improve the management of achondroplasia in Spain through a comprehensive and interdisciplinary approach.
Authors
- José Manuel Rodríguez Domingo (ORCID: https://orcid.org/0000-0001-5714-0766)
- Isolina Riaño Galán (ORCID: https://orcid.org/0000-0003-2125-5101)
- Ana Coral Barreda Bonis (ORCID: https://orcid.org/0009-0000-9810-2854)
- Isabel Leiva‐Gea (ORCID: https://orcid.org/0000-0002-2259-7253)
- Enrique Galán‐Gómez
- Encarna Guillén‐Navarro (ORCID: https://orcid.org/0000-0002-2915-7381)
Institutions
- Universidad de Oviedo (ES)
- Hospital Universitario La Paz (ES)
- Hospital Regional Universitario de Málaga (ES)
- Unidad de Cirugía Artroscópica (ES)
- Centro de Implantología Cirugía Oral y Maxilofacial (ES)
- Instituto Murciano de Investigación Biosanitaria (ES)
- Instituto de Investigación Biomédica de Málaga (ES)
- Instituto de Investigación Sanitaria del Principado de Asturias (ES)
Publication Details
- Journal
- Anales de Pediatría (English Edition)
- Published
- 2024-12-01
- DOI
- https://doi.org/10.1016/j.anpede.2024.09.012
- Citations
- 1
- Primary Topic
- Connective tissue disorders research
- Type
- article
- Field-Weighted Citation Impact
- 0.55
Funders
- BioMarin Pharmaceutical