Outcomes of Modulator Therapy Discontinued After Short‐Term Use in Adult Cystic Fibrosis
This study revealed that CFTR-MTs are effective even in the short term for adult CF patients, but their beneficial effects quickly diminish after discontinuation. Real-life data obtained as a result of discontinuation of drugs due to reimbursement problems has highlighted the significance of regular and uninterrupted use of modulators.
Authors
- Ebru Öztürk (ORCID: https://orcid.org/0000-0001-9206-6856)
- Oğuz Karcıoğlu (ORCID: https://orcid.org/0000-0002-6071-0851)
- Ebru Damadoğlu (ORCID: https://orcid.org/0000-0001-6250-2100)
- Aytekin İdikut (ORCID: https://orcid.org/0000-0002-5750-1223)
Institutions
- Hacettepe University (TR)
Publication Details
- Journal
- Pediatric Pulmonology
- Published
- 2024-11-28
- DOI
- https://doi.org/10.1002/ppul.27416
- Citations
- 1
- Primary Topic
- Cystic Fibrosis Research Advances
- Type
- article
- Field-Weighted Citation Impact
- 0.42