UKHCDO gene therapy taskforce: Guidance for implementation of haemophilia gene therapy into routine clinical practice for adults
These guidelines provide a structured framework for the delivery of liver-directed gene therapy. Whilst specific to the United Kingdom they provide a framework for the implementation of gene therapy in other countries for haemophilia and other monogenic disorders.
Authors
- Debra Pollard (ORCID: https://orcid.org/0000-0002-7797-3500)
- Gillian Lowe (ORCID: https://orcid.org/0000-0003-2527-9557)
- Kathryn Musgrave (ORCID: https://orcid.org/0000-0003-4984-475X)
- Nicola Dunn
- Stephen Classey
- Sara Boyce (ORCID: https://orcid.org/0000-0002-0671-3269)
- David Hopper (ORCID: https://orcid.org/0000-0002-5473-5753)
- Annette Bowyer (ORCID: https://orcid.org/0000-0003-3425-5848)
- Sarah Whitaker (ORCID: https://orcid.org/0000-0002-2528-5829)
- April Jones
- Paul Batty (ORCID: https://orcid.org/0000-0002-7808-3462)
- Jayashree Motwani
- Beatriz Durán
- Pratima Chowdary
- Bahareh Amirloo
Institutions
- Guy's and St Thomas' NHS Foundation Trust (GB)
- Queen Elizabeth Hospital Birmingham (GB)
- Royal Victoria Infirmary (GB)
- The Royal Free Hospital (GB)
- Newcastle upon Tyne Hospitals NHS Foundation Trust (GB)
- Royal Hallamshire Hospital (GB)
- University Hospital Southampton NHS Foundation Trust (GB)
- University of Oxford (GB)
- Basingstoke and North Hampshire Hospital (GB)
- Manchester University NHS Foundation Trust (GB)
- Birmingham Children's Hospital (GB)
- Oxford University Hospitals NHS Trust (GB)
- University College London (GB)
Publication Details
- Journal
- Haemophilia
- Published
- 2024-11-20
- DOI
- https://doi.org/10.1111/hae.15125
- Citations
- 12
- Primary Topic
- Virus-based gene therapy research
- Type
- article
- Field-Weighted Citation Impact
- 6.60
Funders
- Medical Research Council