Pharmacological rescue of the G85E CFTR variant by preclinical and approved modulators

In conclusion, our studies suggest that novel combinations of modulators, endowed with higher efficacy leading to increased rescue of G85E-CFTR, are needed to improve the clinical benefit in patients for this variant.

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Publication Details

Journal
Frontiers in Pharmacology
Published
2024-11-18
DOI
https://doi.org/10.3389/fphar.2024.1494327
Citations
3
Primary Topic
Cystic Fibrosis Research Advances
Type
article
Field-Weighted Citation Impact
1.26

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article

Pharmacological rescue of the G85E CFTR variant by preclinical and approved modulators

Renata Bocciardi, Stefano Costa, Emanuela Pesce, Pietro Ripani et al.
3 citations
Frontiers in Pharmacology
Cystic Fibrosis Research Advances
1.26
article

Pharmacological rescue of the G85E CFTR variant by preclinical and approved modulators

Renata Bocciardi, Stefano Costa, Emanuela Pesce, Pietro Ripani, Federico Cresta, Cristina Fevola, Cristina Pastorino, Tiziano Bandiera, Maria Cristina Lucanto, Elvira Sondo, Vito Terlizzi, Nicoletta Pedemonte, Federico Zara, Luis J. V. Galietta, Anna Borrelli, Stefano Pantano, Mariateresa Lena, Francesca Collini, Valeria Tomati, Valeria Capurro, Carlo Castellani
article en
3 citations

Abstract

In conclusion, our studies suggest that novel combinations of modulators, endowed with higher efficacy leading to increased rescue of G85E-CFTR, are needed to improve the clinical benefit in patients for this variant.

Frontiers in PharmacologyVol. 15
Istituto Giannina Gaslini (IT), Italian Institute of Technology (IT), Cystic Fibrosis Research Foundation (IT), Meyer Children's Hospital (IT), Azienda Ospedaliera Universitaria Policlinico "G. Martino" (IT), Telethon Institute Of Genetics And Medicine (IT), Istituti di Ricovero e Cura a Carattere Scientifico (IT), University of Genoa (IT)
Cystic Fibrosis Foundation, Ministero della Salute, Fondazione per la Ricerca sulla Fibrosi Cistica
Openalex Percentile: Top 18%
Cystic Fibrosis Research Advances
1.26
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