A Retrospective Claims Analysis of the Rate of Complications in Patients Undergoing Treatment for Paroxysmal Nocturnal Hemoglobinuria
The high number of patients with PNH receiving treatment who nevertheless experienced complications demonstrates significant unmet medical need. Further analysis with larger sample sizes and including newer therapies, such as pegcetacoplan and iptacopan, is required to fully understand the scope and magnitude of this unmet need.
Authors
- Yuling Shi (ORCID: https://orcid.org/0000-0002-1273-7881)
- Jason Shafrin (ORCID: https://orcid.org/0000-0001-8444-5979)
- Denise Clayton (ORCID: https://orcid.org/0000-0001-9195-8924)
- Lincy Geevarghese
- Glorian Yen (ORCID: https://orcid.org/0000-0002-3874-7789)
- Anem Waheed (ORCID: https://orcid.org/0000-0001-9957-0721)
Institutions
- Harvard University (US)
- Massachusetts General Hospital (US)
- Novartis (United States) (US)
- Center for the Study of Healthcare Provider Behavior (US)
Publication Details
- Journal
- Advances in Therapy
- Published
- 2024-11-05
- DOI
- https://doi.org/10.1007/s12325-024-03001-w
- Primary Topic
- Complement system in diseases
- Type
- article
- Field-Weighted Citation Impact
- 0.00
Funders
- Novartis Pharmaceuticals Corporation