Mortality, Clinical Complications, and Healthcare Resource Utilization Associated with Managing Transfusion-Dependent β-Thalassemia and Sickle Cell Disease with Recurrent Vaso-occlusive Crises in Italy
Management of TDT and SCD in Italy is associated with significant clinical and health system burden, highlighting the need for new treatments that eliminate RBCTs and VOCs.
Authors
- Nanxin Li (ORCID: https://orcid.org/0009-0006-4412-0997)
- C. Udeze (ORCID: https://orcid.org/0009-0002-7840-6804)
- Chiara Veronesi (ORCID: https://orcid.org/0000-0003-2852-2022)
- Melania Dovizio
- Gian Luca Forni (ORCID: https://orcid.org/0000-0001-9833-1016)
- Luca Degli Esposti
- Thi Xuan Mai Patricia Dang
Institutions
- Società Italiana di Fisica (IT)
- Vertex Pharmaceuticals (United States) (US)
Publication Details
- Journal
- PharmacoEconomics - Open
- Published
- 2024-10-28
- DOI
- https://doi.org/10.1007/s41669-024-00532-4
- Primary Topic
- Hemoglobinopathies and Related Disorders
- Type
- article
- Field-Weighted Citation Impact
- 0.00
Funders
- Vertex Pharmaceuticals