Evaluating the benefits of emicizumab prophylaxis for haemophilia A with inhibitors: A cost‐effectiveness and budget impact analysis in Thailand's upper‐middle income setting

Managing haemophilia A (HA) with inhibitors in Thailand, an upper-middle-income country, faces challenges due to limited access to effective treatments or newer drugs for bleeding management. Emicizumab prophylaxis found to as a cost-effective and viable alternative to traditional treatments, effectively preventing bleeding in Thai HA patients over 2 years old with inhibitors. Demonstrating improved clinical outcomes and reduced costs, emicizumab prophylaxis outperforms episodic BPA treatments, positioning it as a superior treatment option for HA patients with inhibitors in Thailand.

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Publication Details

Journal
Haemophilia
Published
2024-10-05
DOI
https://doi.org/10.1111/hae.15105
Citations
1
Primary Topic
Hemophilia Treatment and Research
Type
article
Field-Weighted Citation Impact
0.45
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article

Evaluating the benefits of emicizumab prophylaxis for haemophilia A with inhibitors: A cost‐effectiveness and budget impact analysis in Thailand's upper‐middle income setting

Preyanate Wilairat, Kirati Kengkla, Pochamana Phisalprapa, Surasak Saokaew et al.
1 citations
Haemophilia
Hemophilia Treatment and Research
0.45
article

Evaluating the benefits of emicizumab prophylaxis for haemophilia A with inhibitors: A cost‐effectiveness and budget impact analysis in Thailand's upper‐middle income setting

Preyanate Wilairat, Kirati Kengkla, Pochamana Phisalprapa, Surasak Saokaew, Rungrote Natesirinilkul, Darintr Sosothikul
article en
1 citations

Abstract

Managing haemophilia A (HA) with inhibitors in Thailand, an upper-middle-income country, faces challenges due to limited access to effective treatments or newer drugs for bleeding management. Emicizumab prophylaxis found to as a cost-effective and viable alternative to traditional treatments, effectively preventing bleeding in Thai HA patients over 2 years old with inhibitors. Demonstrating improved clinical outcomes and reduced costs, emicizumab prophylaxis outperforms episodic BPA treatments, positioning it as a superior treatment option for HA patients with inhibitors in Thailand.

HaemophiliaVol. 30(6)
Thai Red Cross Society (TH), Siriraj Hospital (TH), Chulalongkorn University (TH), Mahidol University (TH), King Chulalongkorn Memorial Hospital (TH), University of Phayao (TH), Chiang Mai University (TH)
Reduced inequalities
Openalex Percentile: Top 32%
Hemophilia Treatment and Research
0.45
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Evaluating the benefits of emicizumab prophylaxis for haemophilia A with inhibitors: A cost‐effectiveness and budget impact analysis in Thailand's upper‐middle income setting — Preyanate Wilairat, Kirati Kengkla, et al. · Haemophilia (2024) | TGRS Research Map | TGRS