Rare Disease Innovation at the FDA—Opportunities for Implementation
This Viewpoint discusses new pathways for researchers to seek collaboration when conducting studies on treatments for rare diseases and conditions.
Authors
- Jeffrey Kahn (ORCID: https://orcid.org/0000-0001-8618-4776)
- Carolyn Shore (ORCID: https://orcid.org/0000-0002-5988-5128)
- Tequam Worku
Institutions
- Johns Hopkins University (US)
- National Academies of Sciences, Engineering, and Medicine (US)
- Johns Hopkins Berman Institute of Bioethics (US)
Publication Details
- Journal
- JAMA
- Published
- 2024-10-02
- DOI
- https://doi.org/10.1001/jama.2024.20358
- Citations
- 6
- Primary Topic
- Genomics and Rare Diseases
- Type
- article
- Field-Weighted Citation Impact
- 3.30