Comparison of Reporting Quality in National Cystic Fibrosis Patient Registries: Implications for Identifying Use of Novel CFTR Modulators
Both F508del prevalence and GDP are associated with variable CFTRm usage rates, although a predominant reason is unclear as a result of poor consistency in registry reporting. Urgent action is needed to create uniform reporting of registry data and increase availability of novel CFTRm therapies to the global CF population.
Authors
- Owen W. Tomlinson (ORCID: https://orcid.org/0000-0003-4063-7682)
- Craig Anthony Williams (ORCID: https://orcid.org/0000-0002-1740-6248)
- Philip Mitchelmore (ORCID: https://orcid.org/0000-0002-7850-3068)
Institutions
- University of Exeter (GB)
- Royal Devon & Exeter NHS Foundation Trust (GB)
Publication Details
- Journal
- Pulmonary Therapy
- Published
- 2024-09-27
- DOI
- https://doi.org/10.1007/s41030-024-00274-y
- Citations
- 1
- Primary Topic
- Cystic Fibrosis Research Advances
- Type
- article
- Field-Weighted Citation Impact
- 0.42