Establishing Clinical Trial Endpoints in Selecting Patients for RPGR Retinal Gene Therapy
Biomarkers of visual function in RPGR-associated RP may lead to identification of appropriate patients for enrollment in clinical trials.
Authors
- Amandeep S. Josan (ORCID: https://orcid.org/0000-0003-1808-6546)
- Robert E. MacLaren (ORCID: https://orcid.org/0000-0002-3096-4682)
- Jasmina Cehajic‐Kapetanovic (ORCID: https://orcid.org/0000-0002-9956-6412)
- Evita Evangelia Christou (ORCID: https://orcid.org/0000-0002-7959-4854)
Institutions
- Nuffield Orthopaedic Centre (GB)
- University of Oxford (GB)
- Oxford University Hospitals NHS Trust (GB)
Publication Details
- Journal
- Translational Vision Science & Technology
- Published
- 2024-09-17
- DOI
- https://doi.org/10.1167/tvst.13.9.18
- Citations
- 5
- Primary Topic
- Retinal Development and Disorders
- Type
- article
- Field-Weighted Citation Impact
- 1.17
Funders
- Biogen
- National Institute for Health and Care Research
- University of Oxford
- Medical Research Council
- NIHR Oxford Biomedical Research Centre