Validating new symptom emergence as a patient-centric outcome measure for PD clinical trials

Further validation using data sets with frequent administration of MDS-UPDRS is necessary to assess value of this approach as an outcome measure in PD clinical trials.

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Publication Details

Journal
Parkinsonism & Related Disorders
Published
2024-09-10
DOI
https://doi.org/10.1016/j.parkreldis.2024.107118
Primary Topic
Parkinson's Disease Mechanisms and Treatments
Type
article
Field-Weighted Citation Impact
0.00

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article

Validating new symptom emergence as a patient-centric outcome measure for PD clinical trials

Haotian Zou, Jesse M. Cedarbaum, Glenn T. Stebbins, Tanya Simuni et al.
Parkinsonism & Related Disorders
Parkinson's Disease Mechanisms and Treatments
article

Validating new symptom emergence as a patient-centric outcome measure for PD clinical trials

Haotian Zou, Jesse M. Cedarbaum, Glenn T. Stebbins, Tanya Simuni, Sheng Luo
article en

Abstract

Further validation using data sets with frequent administration of MDS-UPDRS is necessary to assess value of this approach as an outcome measure in PD clinical trials.

Parkinsonism & Related DisordersVol. 128
Northwestern University (US), Rush University Medical Center (US), Duke University (US), Yale University (US)
Michael J. Fox Foundation for Parkinson's Research, Parkinson's Disease Foundation, Eli Lilly and Company, Pfizer, Sanofi, Biogen, Davis Phinney Foundation, Neurocrine Biosciences, Denali Therapeutics, Amneal Pharmaceuticals, University of Oxford, Newcastle University, University of Glasgow, IXICO, National Institute of Neurological Disorders and Stroke
Openalex Percentile: Top 76%
Parkinson's Disease Mechanisms and Treatments
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