Effectiveness of Nusinersen in Adolescents and Adults with Spinal Muscular Atrophy: Systematic Review and Meta-analysis
Findings provide consolidated evidence that nusinersen is effective in improving or stabilizing motor function in many adolescents and adults with a broad spectrum of SMA.
Authors
- Bora Youn (ORCID: https://orcid.org/0000-0003-2870-976X)
- Angela D. Paradis (ORCID: https://orcid.org/0000-0001-5698-8802)
- Giorgia Coratti (ORCID: https://orcid.org/0000-0001-6666-5628)
- Tim Hagenacker (ORCID: https://orcid.org/0000-0002-3631-3450)
- Eugenio Maria Mercuri (ORCID: https://orcid.org/0000-0002-9851-5365)
- Lorenzo Maggi (ORCID: https://orcid.org/0000-0002-0932-5173)
- Stephanie Raynaud
Institutions
- Università Cattolica del Sacro Cuore (IT)
- Biogen (United States) (US)
- Essen University Hospital (DE)
- Fondazione IRCCS Istituto Neurologico Carlo Besta (IT)
Publication Details
- Journal
- Neurology and Therapy
- Published
- 2024-09-02
- DOI
- https://doi.org/10.1007/s40120-024-00653-2
- Citations
- 25
- Primary Topic
- Neurogenetic and Muscular Disorders Research
- Type
- article
- Field-Weighted Citation Impact
- 10.95
Funders
- Biogen