Hematopoietic stem cell transplantation for CTLA-4 insufficiency across Europe: A European Society for Blood and Marrow Transplantation Inborn Errors Working Party study
HSCT is an effective therapy to prevent ongoing disease progression and morbidity, with improving survival rates over time and in patients with lower pre-HSCT disease activity.
Authors
- Emma Morris (ORCID: https://orcid.org/0000-0003-4834-1130)
- Carsten Speckmann (ORCID: https://orcid.org/0000-0002-6217-1556)
- Krzysztof Kałwak (ORCID: https://orcid.org/0000-0003-1174-5799)
- Alexandra Laberko (ORCID: https://orcid.org/0000-0002-2354-2588)
- Bénédicte Neven (ORCID: https://orcid.org/0000-0001-8941-0935)
- Andrew R. Gennery (ORCID: https://orcid.org/0000-0002-6218-1324)
- Rosie Hague
- Katarzyna Drabko (ORCID: https://orcid.org/0000-0002-7094-9129)
- Fabian Hauck (ORCID: https://orcid.org/0000-0001-9644-2003)
- Su Han Lum (ORCID: https://orcid.org/0000-0002-5471-029X)
- Thomas A. Fox (ORCID: https://orcid.org/0000-0002-1163-2295)
- Michele Malagola (ORCID: https://orcid.org/0000-0003-0907-130X)
- Michael H. Albert (ORCID: https://orcid.org/0000-0001-9143-3263)
- Anna-Maria Ewins
- Emilie P. Buddingh (ORCID: https://orcid.org/0000-0002-2755-9408)
- Christo Tsilifis (ORCID: https://orcid.org/0000-0002-1368-104X)
- Christina Oikonomopoulou (ORCID: https://orcid.org/0000-0003-2053-0191)
- Vassilios Lougaris (ORCID: https://orcid.org/0000-0003-2303-9533)
- Yasmina Mozo (ORCID: https://orcid.org/0000-0002-5666-1911)
- Petr Sedláček (ORCID: https://orcid.org/0000-0002-6211-9643)
- Venetia Bigley (ORCID: https://orcid.org/0000-0002-3017-2474)
- Jennifer M.L. Tjon (ORCID: https://orcid.org/0000-0002-2393-715X)
- Arjan C. Lankester (ORCID: https://orcid.org/0000-0002-6703-2993)
- Bodo Grimbacher (ORCID: https://orcid.org/0000-0002-6897-6806)
- Suzanne Elcombe (ORCID: https://orcid.org/0009-0005-7455-9477)
- Robert Wynn (ORCID: https://orcid.org/0000-0002-6046-8428)
- Mary Slatter
- Claudia Wehr (ORCID: https://orcid.org/0000-0002-5037-6175)
- Dolores Corral
- Adriana Margarit
Institutions
- Medical University of Lublin (PL)
- Hôpital Necker-Enfants Malades (FR)
- Hospital Sant Joan de Déu Barcelona (ES)
- University College London Hospitals NHS Foundation Trust (GB)
- Charles University (CZ)
- Leiden University Medical Center (NL)
- Royal Hospital for Children (GB)
- Hospital Universitario La Paz (ES)
- University Medical Center Freiburg (DE)
- Newcastle upon Tyne Hospitals NHS Foundation Trust (GB)
- Wroclaw Medical University (PL)
- Azienda Socio Sanitaria Territoriale degli Spedali Civili di Brescia (IT)
- Children's Hospital Agia Sophia (GR)
- Dmitry Rogachev National Research Center of Pediatric Hematology, Oncology and Immunology (RU)
- Willem-Alexander Kinderziekenhuis (NL)
- Great North Children's Hospital (GB)
- Royal Manchester Children's Hospital (GB)
- University College London (GB)
- University of Brescia (IT)
- Ludwig-Maximilians-Universität München (DE)
Publication Details
- Journal
- Journal of Allergy and Clinical Immunology
- Published
- 2024-08-30
- DOI
- https://doi.org/10.1016/j.jaci.2024.08.020
- Citations
- 13
- Primary Topic
- Immunodeficiency and Autoimmune Disorders
- Type
- article
- Field-Weighted Citation Impact
- 3.13
Funders
- National Institute for Health and Care Research
- Medical Research Council
- UCLH Biomedical Research Centre