Antisense Oligonucleotide Therapy for Calmodulinopathy

These results provide proof of concept that ASOs targeting individual calmodulin genes are potentially effective and safe therapies for calmodulinopathies.

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Publication Details

Journal
Circulation
Published
2024-08-19
DOI
https://doi.org/10.1161/circulationaha.123.068111
Citations
11
Primary Topic
Cardiac electrophysiology and arrhythmias
Type
article
Field-Weighted Citation Impact
4.42
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article

Antisense Oligonucleotide Therapy for Calmodulinopathy

Michael A. Trembley, Sanda Alexandrescu, Fujian Lu, Chrystalle Katte Carreon et al.
11 citations
Circulation
Cardiac electrophysiology and arrhythmias
4.42
article

Antisense Oligonucleotide Therapy for Calmodulinopathy

Michael A. Trembley, Sanda Alexandrescu, Fujian Lu, Chrystalle Katte Carreon, Peter T. Sage, Carter Liou, C. Park, Adam E. Mullick, Maksymilian Prondzynski, Michael Rubart, Qing Ma, Cecília B. Cavazzoni, Shuai Guo, Nikoleta Pavlaki, Raul Hernandes Bortolin, Daisuke Yoshinaga, Juan Putra, Jiehui Chen, Vassilios J. Bezzerides, Dieter A. Kubli, Wen‐Chin Tsai, Peizhe Wang, Erin Keating, Mason Sweat, Dominic James Abrams, Robert Whitehill, William T. Pu, Paul Berkson, Farina Nawar, Thomas Samenuk
article en
11 citations

Abstract

These results provide proof of concept that ASOs targeting individual calmodulin genes are potentially effective and safe therapies for calmodulinopathies.

CirculationVol. 150(15)
Brigham and Women's Hospital (US), Boston Children's Hospital (US), Harvard University (US), Ionis Pharmaceuticals (United States) (US), San Diego Cardiac Center (US), Children's Healthcare of Atlanta (US), Hesco (United States) (US), Harvard Stem Cell Institute (US), Indiana University – Purdue University Indianapolis (US)
Good health and well-being
Openalex Percentile: Top 5%
Cardiac electrophysiology and arrhythmias
4.42
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