Antisense Oligonucleotide Therapy for Calmodulinopathy
These results provide proof of concept that ASOs targeting individual calmodulin genes are potentially effective and safe therapies for calmodulinopathies.
Authors
- Michael A. Trembley (ORCID: https://orcid.org/0000-0001-6675-9325)
- Sanda Alexandrescu (ORCID: https://orcid.org/0000-0001-9246-4184)
- Fujian Lu (ORCID: https://orcid.org/0000-0003-3605-3924)
- Chrystalle Katte Carreon (ORCID: https://orcid.org/0000-0003-2152-7998)
- Peter T. Sage (ORCID: https://orcid.org/0000-0002-7287-0326)
- Carter Liou (ORCID: https://orcid.org/0009-0000-2577-4350)
- C. Park
- Adam E. Mullick (ORCID: https://orcid.org/0000-0003-4600-961X)
- Maksymilian Prondzynski (ORCID: https://orcid.org/0000-0002-6846-6435)
- Michael Rubart (ORCID: https://orcid.org/0000-0002-7386-6943)
- Qing Ma (ORCID: https://orcid.org/0000-0002-5625-1330)
- Cecília B. Cavazzoni (ORCID: https://orcid.org/0000-0003-2113-6620)
- Shuai Guo (ORCID: https://orcid.org/0000-0002-9368-0548)
- Nikoleta Pavlaki (ORCID: https://orcid.org/0000-0001-5484-192X)
- Raul Hernandes Bortolin (ORCID: https://orcid.org/0000-0003-3424-3281)
- Daisuke Yoshinaga (ORCID: https://orcid.org/0000-0003-0484-510X)
- Juan Putra (ORCID: https://orcid.org/0000-0002-3487-4641)
- Jiehui Chen (ORCID: https://orcid.org/0000-0002-0550-2195)
- Vassilios J. Bezzerides (ORCID: https://orcid.org/0000-0003-0825-6580)
- Dieter A. Kubli (ORCID: https://orcid.org/0000-0001-7970-4075)
- Wen‐Chin Tsai (ORCID: https://orcid.org/0000-0001-8648-9414)
- Peizhe Wang (ORCID: https://orcid.org/0000-0003-4298-2471)
- Erin Keating
- Mason Sweat (ORCID: https://orcid.org/0000-0002-5400-1266)
- Dominic James Abrams (ORCID: https://orcid.org/0000-0001-5266-2805)
- Robert Whitehill (ORCID: https://orcid.org/0000-0002-3810-7132)
- William T. Pu (ORCID: https://orcid.org/0000-0002-4551-8079)
- Paul Berkson
- Farina Nawar
- Thomas Samenuk (ORCID: https://orcid.org/0000-0001-9651-4433)
Institutions
- Brigham and Women's Hospital (US)
- Boston Children's Hospital (US)
- Harvard University (US)
- Ionis Pharmaceuticals (United States) (US)
- San Diego Cardiac Center (US)
- Children's Healthcare of Atlanta (US)
- Hesco (United States) (US)
- Harvard Stem Cell Institute (US)
- Indiana University – Purdue University Indianapolis (US)
Publication Details
- Journal
- Circulation
- Published
- 2024-08-19
- DOI
- https://doi.org/10.1161/circulationaha.123.068111
- Citations
- 11
- Primary Topic
- Cardiac electrophysiology and arrhythmias
- Type
- article
- Field-Weighted Citation Impact
- 4.42