BRAF and MEK inhibitor targeted therapy in papillary craniopharyngiomas: a cohort study
In this study, 94% of patients showed partial response or better to TT. Adverse events were acceptable. Further research is needed to establish standardized protocols; however, these results advocate for a NEO approach in invasive PCPs.
Authors
- Dario De Alcubierre (ORCID: https://orcid.org/0000-0001-5242-1761)
- Bertrand Baussart (ORCID: https://orcid.org/0000-0003-0735-8278)
- Alexandre Vasiljevic (ORCID: https://orcid.org/0000-0001-5954-0317)
- Philippe Chanson (ORCID: https://orcid.org/0000-0001-5096-5722)
- C. Mouly (ORCID: https://orcid.org/0000-0003-4393-5351)
- Gérald Raverot (ORCID: https://orcid.org/0000-0002-9517-338X)
- Chiara Villa (ORCID: https://orcid.org/0000-0001-6245-4487)
- François Ducray (ORCID: https://orcid.org/0000-0002-8150-5785)
- Camille Sergeant (ORCID: https://orcid.org/0009-0009-8182-5955)
- Delphine Larrieu‐Ciron (ORCID: https://orcid.org/0000-0002-0478-7774)
- Grigorios Gkasdaris (ORCID: https://orcid.org/0000-0002-7877-2743)
- Claire Briet
- Anthony Joncour
- Julien Boetto (ORCID: https://orcid.org/0000-0003-2572-8594)
- Emmanuel Jouanneau (ORCID: https://orcid.org/0000-0003-2506-3430)
- Margaux Mordrel
- L. Feuvret (ORCID: https://orcid.org/0000-0001-6820-2782)
- Fabien Almairac
Institutions
- Université Claude Bernard Lyon 1 (FR)
- Centre National de la Recherche Scientifique (FR)
- Inserm (FR)
- Université de Montpellier (FR)
- Université Paris Cité (FR)
- Université Paris-Saclay (FR)
- Université de Poitiers (FR)
- Sorbonne Université (FR)
- Assistance Publique – Hôpitaux de Paris (FR)
- Hospices Civils de Lyon (FR)
- Hôpital Gui de Chauliac (FR)
- Centre Hospitalier Universitaire d'Angers (FR)
- Pitié-Salpêtrière Hospital (FR)
- Centre de Recherche en Cancérologie de Lyon (FR)
- Institut Cochin (FR)
- Hôpital Pasteur (FR)
- Bicêtre Hospital (FR)
- Sapienza University of Rome (IT)
Publication Details
- Journal
- European Journal of Endocrinology
- Published
- 2024-08-01
- DOI
- https://doi.org/10.1093/ejendo/lvae091
- Citations
- 19
- Primary Topic
- Pituitary Gland Disorders and Treatments
- Type
- article
- Field-Weighted Citation Impact
- 6.80