Efficacy and Safety of Branched Chain Amino Acids on Retinitis Pigmentosa: A Randomized, Double-Blind, Placebo-Controlled Clinical Trial
Our study demonstrates the safety of administering BCAAs to patients with RP. Accordingly, larger, more homogeneous clinical studies with longer durations may suggest their potential as therapeutic agents.
Authors
- Yoko Amino
- Hanako Ohashi Ikeda (ORCID: https://orcid.org/0000-0001-9572-8659)
- Manabu Miyata (ORCID: https://orcid.org/0000-0002-7574-1749)
- Takayuki Nakagawa (ORCID: https://orcid.org/0000-0003-1890-0843)
- Akitaka Tsujikawa (ORCID: https://orcid.org/0000-0003-0779-7799)
- Hiroyasu Abe
- Harue Tada (ORCID: https://orcid.org/0000-0001-8634-5592)
- Akio Oishi (ORCID: https://orcid.org/0000-0002-0977-9458)
- Tomoko Hasegawa (ORCID: https://orcid.org/0000-0002-5539-0099)
- Satoshi Morita (ORCID: https://orcid.org/0000-0002-4344-3317)
Institutions
- Japan Society for the Promotion of Science (JP)
- Kyoto University (JP)
- Kyoto University Hospital (JP)
- Nagasaki University (JP)
Publication Details
- Journal
- Translational Vision Science & Technology
- Published
- 2024-08-16
- DOI
- https://doi.org/10.1167/tvst.13.8.29
- Citations
- 5
- Primary Topic
- Retinal Development and Disorders
- Type
- article
- Field-Weighted Citation Impact
- 1.17
Funders
- Japan Agency for Medical Research and Development
- EA Pharma Co., Ltd.