Ganaxolone (Ztalmy) for CDKL5 Deficiency Disorder
The FDA has approved ganaxolone (Ztalmy – Marinus) for oral treatment of seizures associated with cyclin-dependent kinase-like 5 (CDKL5) deficiency disorder in patients ≥2 years old. It is the first drug to be approved in the US for this indication.
Publication Details
- Journal
- The medical letter on drugs and therapeutics/The medical letter
- Published
- 2024-08-15
- DOI
- https://doi.org/10.58347/tml.2024.1709g
- Primary Topic
- Genetics and Neurodevelopmental Disorders
- Type
- article
- Field-Weighted Citation Impact
- 0.00